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Etid klinik pou Maladi Depo Glikojèn Tip II nan Virginia
6 etid pou Maladi Depo Glikojèn Tip II ap chèche patisipan nan sit nan Virginia.
Vil nan Virginia
Tèks ofisyèl etid la (Anglè)
A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of DNL952 in Adult Participants With Late-Onset Pompe Disease
- The Lysosomal & Rare Disorders Research & Treatment Center, Fairfax
Ap rekriteFaz 1
Laj 18 a 75 · Tout sèks · Mizajou Aug 17, 2026 · NCT07354724A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)
- Virginia Commonwealth University (VCU), Richmond
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Laj 18 a 65 · Tout sèks · Mizajou Jul 20, 2026 · NCT07282847Pompe Disease Registry Protocol
- O & O Alpan- Site Number : 840025, Fairfax
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Jun 23, 2026 · NCT00231400Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)
- Lysosomal and Rare Disorders Research and Treatment Center (LDRTC), Fairfax
Ap rekriteFaz 2
Laj 18 ak plis · Tout sèks · Mizajou Jun 23, 2026 · NCT07123155Pompe Pregnancy Sub-Registry
- O & O Alpan- Site Number : 840025, Fairfax
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Tout laj · Fanm · Mizajou Apr 16, 2026 · NCT00567073A Global Prospective Observational Registry of Patients With Pompe Disease
- Lysosomal and Rare Disorders Research and Treatment Center, Inc., Fairfax
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Mar 10, 2026 · NCT06121011Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.