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Etid klinik pou Maladi Depo Glikojèn ap rekrite nan Etazini
5 etid pou Maladi Depo Glikojèn ap rekrite patisipan nan sit atravè Etazini.
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ATR 1072 in Participants With PRKAG2 Syndrome
Ap rekriteFaz 1/2
Laj 18 a 65 · Tout sèks · Mizajou Sep 18, 2026 · NCT07738107A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)
Ap rekriteFaz 1/2
Laj 18 a 65 · Tout sèks · Mizajou Jul 20, 2026 · NCT07282847Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)
Ap rekriteFaz 2
Laj 18 ak plis · Tout sèks · Mizajou Jun 23, 2026 · NCT07123155Rare Glycogen Storage Diseases Natural History Study
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Laj 0 a 90 · Tout sèks · Mizajou Jan 7, 2026 · NCT06795152Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou May 29, 2025 · NCT01793168Sous ClinicalTrials.gov, done yo ranmase Oct 2, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.