Akèy › Maladi Depo Glikojèn › North Carolina
Etid klinik pou Maladi Depo Glikojèn nan North Carolina
3 etid pou Maladi Depo Glikojèn ap chèche patisipan nan sit nan North Carolina.
Vil nan North Carolina
Tèks ofisyèl etid la (Anglè)
A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)
- Duke University, Durham
Ap rekriteFaz 1/2
Laj 18 a 65 · Tout sèks · Mizajou Jul 20, 2026 · NCT07282847Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)
- Duke University Medical Center, Durham
Ap rekriteFaz 2
Laj 18 ak plis · Tout sèks · Mizajou Jun 23, 2026 · NCT07123155Rare Glycogen Storage Diseases Natural History Study
- Duke University, Durham
Ap rekriteEtid obsèvasyon
Laj 0 a 90 · Tout sèks · Mizajou Jan 7, 2026 · NCT06795152Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.