Akèy › Erè Metabolism Konjenital
Etid klinik pou Erè Metabolism Konjenital ap rekrite nan Etazini
11 etid pou Erè Metabolism Konjenital ap rekrite patisipan nan sit atravè Etazini.
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Etid ki fèk mete ajou
Tèks ofisyèl etid la (Anglè)
Natural History, Physiology, Microbiome and Biochemistry Studies of Propionic Acidemia
Ap rekriteEtid obsèvasyonVolontè an sante akeyi
1 Month – 100 Years · Tout sèks · Mizajou Sep 28, 2026 · NCT02890342A Long-Term Observational Study of Patients With Fucosidosis
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Sep 17, 2026 · NCT07615400Clinical and Laboratory Study of Methylmalonic Acidemia
Ap rekriteEtid obsèvasyonVolontè an sante akeyi
1 Month – 115 Years · Tout sèks · Mizajou Sep 10, 2026 · NCT00078078Study of Alkaptonuria
Ap rekriteEtid obsèvasyon
Laj 2 a 115 · Tout sèks · Mizajou Sep 1, 2026 · NCT00005909Long-term Follow-up (LTFU) Study of Participants in Any iECURE Protocol Using an Investigational Product (IP)
Ap rekriteEtid obsèvasyon
7 Months – 15 Months · Tout sèks · Mizajou Aug 31, 2026 · NCT06805695Phase 1/2: CD45RA Depleted Stem Cell Addback to Prevent Viral or Fungal Infections Post TCRab/CD19 Depleted HSCT
Ap rekriteFaz 1/2
1 Month – 25 Years · Tout sèks · Mizajou Apr 15, 2026 · NCT06839456Registry of Patients Diagnosed With Lysosomal Storage Diseases
Ap rekriteEtid obsèvasyon
Jiska laj 64 · Tout sèks · Mizajou Apr 8, 2026 · NCT05619900A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study
Ap rekriteFaz 1/2
Laj 1 ak plis · Tout sèks · Mizajou Mar 23, 2026 · NCT05130437Expanded Access Protocol Using CD3+/CD19+ Depleted PBSC
Ap rekriteFaz 1 bonè
Jiska laj 30 · Tout sèks · Mizajou Feb 20, 2026 · NCT02356653Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia
Ap rekriteFaz 1/2
Tout laj · Tout sèks · Mizajou Jan 22, 2026 · NCT04159103An Extension Study to Evaluate the Long-Term Safety and Clinical Activity of mRNA-3705 in Participants Previously Enrolled in Other Clinical Studies of mRNA-3705
Ap rekriteFaz 1/2
Laj 1 ak plis · Tout sèks · Mizajou Dec 23, 2025 · NCT05295433Sous ClinicalTrials.gov, done yo ranmase Oct 1, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.