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Akèy › Erè Metabolism Konjenital

Etid klinik pou Erè Metabolism Konjenital ap rekrite nan Etazini

11 etid pou Erè Metabolism Konjenital ap rekrite patisipan nan sit atravè Etazini.

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Tèks ofisyèl etid la (Anglè)

Natural History, Physiology, Microbiome and Biochemistry Studies of Propionic Acidemia

Ap rekriteEtid obsèvasyonVolontè an sante akeyi
1 Month – 100 Years · Tout sèks · Mizajou Sep 28, 2026 · NCT02890342

A Long-Term Observational Study of Patients With Fucosidosis

Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Sep 17, 2026 · NCT07615400

Clinical and Laboratory Study of Methylmalonic Acidemia

Ap rekriteEtid obsèvasyonVolontè an sante akeyi
1 Month – 115 Years · Tout sèks · Mizajou Sep 10, 2026 · NCT00078078

Study of Alkaptonuria

Ap rekriteEtid obsèvasyon
Laj 2 a 115 · Tout sèks · Mizajou Sep 1, 2026 · NCT00005909

Long-term Follow-up (LTFU) Study of Participants in Any iECURE Protocol Using an Investigational Product (IP)

Ap rekriteEtid obsèvasyon
7 Months – 15 Months · Tout sèks · Mizajou Aug 31, 2026 · NCT06805695

Phase 1/2: CD45RA Depleted Stem Cell Addback to Prevent Viral or Fungal Infections Post TCRab/CD19 Depleted HSCT

Ap rekriteFaz 1/2
1 Month – 25 Years · Tout sèks · Mizajou Apr 15, 2026 · NCT06839456

Registry of Patients Diagnosed With Lysosomal Storage Diseases

Ap rekriteEtid obsèvasyon
Jiska laj 64 · Tout sèks · Mizajou Apr 8, 2026 · NCT05619900

Expanded Access Protocol Using CD3+/CD19+ Depleted PBSC

Ap rekriteFaz 1 bonè
Jiska laj 30 · Tout sèks · Mizajou Feb 20, 2026 · NCT02356653

Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia

Ap rekriteFaz 1/2
Tout laj · Tout sèks · Mizajou Jan 22, 2026 · NCT04159103

Sous ClinicalTrials.gov, done yo ranmase Oct 1, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.