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Etid klinik pou Erè Metabolism Konjenital nan Kalifòni

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Tèks ofisyèl etid la (Anglè)

A Long-Term Observational Study of Patients With Fucosidosis

  • Children's Hospital of Orange County, Orange
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Sep 17, 2026 · NCT07615400

Registry of Patients Diagnosed With Lysosomal Storage Diseases

  • University of California San Francisco, San Francisco
Ap rekriteEtid obsèvasyon
Jiska laj 64 · Tout sèks · Mizajou Apr 8, 2026 · NCT05619900

A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study

  • Ronald Reagan UCLA Medical Center, Los Angeles
  • University of Stanford Medical Center, Palo Alto
Ap rekriteFaz 1/2
Laj 1 ak plis · Tout sèks · Mizajou Mar 23, 2026 · NCT05130437

Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia

  • UCSD Altman Clinical and Transalational Research Institute Building, Los Angeles
  • Ronald Reagan UCLA Medical Center, Los Angeles
  • Lucile Packard Children's Hospital Stanford, Stanford
Ap rekriteFaz 1/2
Tout laj · Tout sèks · Mizajou Jan 22, 2026 · NCT04159103

An Extension Study to Evaluate the Long-Term Safety and Clinical Activity of mRNA-3705 in Participants Previously Enrolled in Other Clinical Studies of mRNA-3705

  • UCLA Medical Center, Los Angeles
  • Lucile Packard Children's Hospital at Stanford, Palo Alto
  • Altman Clinical and Translational Research Institution, San Diego
Ap rekriteFaz 1/2
Laj 1 ak plis · Tout sèks · Mizajou Dec 23, 2025 · NCT05295433

Sous ClinicalTrials.gov, done yo ranmase Oct 1, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.