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A Study of AAV9 Gene Therapy in Participants With Canavan Disease (CANaspire Clinical Trial)
- UCSF Benioff Children's Hospital Oakland, Oakland
Ap rekriteFaz 1/2
30 Months · Tout sèks · Mizajou Apr 17, 2026 · NCT04998396North American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC)
- University of California San Diego, San Diego
- Lucile Packard Children's Hospital, Stanford
Ap rekriteEtid obsèvasyonVolontè an sante akeyi
Tout laj · Tout sèks · Mizajou Feb 4, 2026 · NCT01694940The Myelin Disorders Biorepository Project
- Children's Hospital of Los Angeles, Los Angeles
- Children's Hospital of Orange County, Orange
- Stanford University (Lucile Packard Children's Hospital), Palo Alto
- ak 3 plis
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Oct 23, 2025 · NCT03047369Natural History Study of Patients with HPDL Mutations
- Eun Hae Lee, San Diego
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Mar 30, 2025 · NCT05848271Sous ClinicalTrials.gov, done yo ranmase Oct 1, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.