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Etid klinik pou Mukopolisakaridoz IV ap rekrite nan Etazini

11 etid pou Mukopolisakaridoz IV ap rekrite patisipan nan sit atravè Etazini.

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Tèks ofisyèl etid la (Anglè)

Uncovering Genes Behind Cartilage Tumors and Vascular Anomalies Using Genomic Sequencing

Ap rekriteEtid obsèvasyon
Laj 2 a 100 · Tout sèks · Mizajou Oct 1, 2026 · NCT06749366

Study of Skeletal Disorders

Ap rekriteEtid obsèvasyonVolontè an sante akeyi
2 Months – 100 Years · Tout sèks · Mizajou Jul 20, 2026 · NCT05031507

Prospective Clinical Assessment Study in Children With Hypochondroplasia

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30 Months – 16 Years · Tout sèks · Mizajou Jul 16, 2026 · NCT06410976

Interventional Study of Infigratinib in Children < 3 Years Old With Achondroplasia (ACH)

Ap rekriteFaz 2
0 Years – 32 Months · Tout sèks · Mizajou Jul 13, 2026 · NCT07169279

Non-invasive Functional Assessment and Pathogenesis of Morquio A

Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou May 13, 2026 · NCT05284006

Effects of Bisphosphonates on OI-Related Hearing Loss

Ap rekriteFaz 4Volontè an sante akeyi
Laj 6 a 100 · Tout sèks · Mizajou Apr 28, 2026 · NCT04152551

Registry of Patients Diagnosed With Lysosomal Storage Diseases

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Jiska laj 64 · Tout sèks · Mizajou Apr 8, 2026 · NCT05619900

PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)

Ap rekriteFaz 1
Laj 18 a 50 · Fanm · Mizajou Mar 17, 2026 · NCT04532047

Longitudinal Study of Neurodegenerative Disorders

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Tout laj · Tout sèks · Mizajou Feb 9, 2026 · NCT03333200

Cardiac Structure and Function in MPS

Ap rekriteEtid obsèvasyonVolontè an sante akeyi
Laj 0 a 99 · Tout sèks · Mizajou Jan 26, 2026 · NCT07361536

Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.