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Akèy › Mukopolisakaridoz IV › Kalifòni

Etid klinik pou Mukopolisakaridoz IV nan Kalifòni

6 etid pou Mukopolisakaridoz IV ap chèche patisipan nan sit nan Kalifòni.

Tèks ofisyèl etid la (Anglè)

Prospective Clinical Assessment Study in Children With Hypochondroplasia

  • UCSF Benioff Children's Hospital, Oakland
Ap rekriteEtid obsèvasyon
30 Months – 16 Years · Tout sèks · Mizajou Jul 16, 2026 · NCT06410976

Interventional Study of Infigratinib in Children < 3 Years Old With Achondroplasia (ACH)

  • UCSF Benioff Children's Hospital, Oakland
Ap rekriteFaz 2
0 Years – 32 Months · Tout sèks · Mizajou Jul 13, 2026 · NCT07169279

A Study Evaluating the Impact of Regular FODMAP-targeting Digestive Enzyme Blend Use on Gastrointestinal Symptoms in Individuals With Self-Reported Bloating

  • People Science, Los Angeles
Ap rekriteVolontè an sante akeyi
Laj 18 ak plis · Tout sèks · Mizajou May 15, 2026 · NCT07591584

Registry of Patients Diagnosed With Lysosomal Storage Diseases

  • University of California San Francisco, San Francisco
Ap rekriteEtid obsèvasyon
Jiska laj 64 · Tout sèks · Mizajou Apr 8, 2026 · NCT05619900

PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)

  • University of California, San Francisco
Ap rekriteFaz 1
Laj 18 a 50 · Fanm · Mizajou Mar 17, 2026 · NCT04532047

Cardiac Structure and Function in MPS

  • Children'S Hospital of Orange County, Orange
Ap rekriteEtid obsèvasyonVolontè an sante akeyi
Laj 0 a 99 · Tout sèks · Mizajou Jan 26, 2026 · NCT07361536

Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.