Akèy › Mukopolisakaridoz IV › Kalifòni
Etid klinik pou Mukopolisakaridoz IV nan Kalifòni
6 etid pou Mukopolisakaridoz IV ap chèche patisipan nan sit nan Kalifòni.
Tèks ofisyèl etid la (Anglè)
Prospective Clinical Assessment Study in Children With Hypochondroplasia
- UCSF Benioff Children's Hospital, Oakland
Ap rekriteEtid obsèvasyon
30 Months – 16 Years · Tout sèks · Mizajou Jul 16, 2026 · NCT06410976Interventional Study of Infigratinib in Children < 3 Years Old With Achondroplasia (ACH)
- UCSF Benioff Children's Hospital, Oakland
Ap rekriteFaz 2
0 Years – 32 Months · Tout sèks · Mizajou Jul 13, 2026 · NCT07169279A Study Evaluating the Impact of Regular FODMAP-targeting Digestive Enzyme Blend Use on Gastrointestinal Symptoms in Individuals With Self-Reported Bloating
- People Science, Los Angeles
Ap rekriteVolontè an sante akeyi
Laj 18 ak plis · Tout sèks · Mizajou May 15, 2026 · NCT07591584Registry of Patients Diagnosed With Lysosomal Storage Diseases
- University of California San Francisco, San Francisco
Ap rekriteEtid obsèvasyon
Jiska laj 64 · Tout sèks · Mizajou Apr 8, 2026 · NCT05619900PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)
- University of California, San Francisco
Ap rekriteFaz 1
Laj 18 a 50 · Fanm · Mizajou Mar 17, 2026 · NCT04532047Cardiac Structure and Function in MPS
- Children'S Hospital of Orange County, Orange
Ap rekriteEtid obsèvasyonVolontè an sante akeyi
Laj 0 a 99 · Tout sèks · Mizajou Jan 26, 2026 · NCT07361536Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.