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Etid klinik pou Maladi ra nan North Carolina

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Vil nan North Carolina

Tèks ofisyèl etid la (Anglè)

Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network

  • Duke University Health System, Durham
Ap rekriteEtid obsèvasyonVolontè an sante akeyi
1 Month – 100 Years · Tout sèks · Mizajou Oct 2, 2026 · NCT02450851

Odevixibat Pregnancy and Lactation Surveillance Program: A Study to Evaluate the Safety of Odevixibat During Pregnancy and/or Lactation

  • Virtual Research Coordination Center Odevixibat (BYLVAY) Pregnancy Surveillance Program, Wilmington
Ap rekriteEtid obsèvasyon
Tout laj · Fanm · Mizajou Oct 1, 2026 · NCT06258902

Elafibranor Pregnancy Surveillance Program: A Study to Evaluate the Safety of Elafibranor During Pregnancy

  • Virtual Research Coordination Center, Wilmington
Ap rekriteEtid obsèvasyon
Tout laj · Fanm · Mizajou Aug 31, 2026 · NCT07556913

A Study Evaluating the Real-World Experience of Givinostat in Patients With Duchenne Muscular Dystrophy

  • Duke University / Lenox Baker Children's Hospital, Durham
Ap rekriteEtid obsèvasyon
Laj 6 ak plis · Tout sèks · Mizajou Jul 2, 2026 · NCT07127978

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

  • Duke University Medical Center, Durham
Ap rekriteFaz 2
Laj 18 ak plis · Tout sèks · Mizajou Jun 23, 2026 · NCT07123155

The ExTINGUISH Trial of Inebilizumab in NMDAR Encephalitis

  • Wake Forest University Health Sciences, Winston-Salem
Ap rekriteFaz 2
Laj 12 ak plis · Tout sèks · Mizajou Jul 1, 2025 · NCT04372615

Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.