🔎 Trials Near Me

Akèy › Maladi ra

Etid klinik pou Maladi ra ap rekrite nan Etazini

33 etid pou Maladi ra ap rekrite patisipan nan sit atravè Etazini.

Vil ki gen plis etid

Pa eta

Etid ki fèk mete ajou

Tèks ofisyèl etid la (Anglè)

A Study of SGT-212 Gene Therapy in Friedreich's Ataxia

Ap rekriteFaz 1
Laj 18 a 40 · Tout sèks · Mizajou Sep 29, 2026 · NCT07180355

RAPA-501 Therapy for ALS

Ap rekriteFaz 2/3
Laj 18 ak plis · Tout sèks · Mizajou Sep 29, 2026 · NCT04220190

Diagnosis and Treatment of Patients With Inborn Errors of Metabolism

Ap rekriteEtid obsèvasyonVolontè an sante akeyi
1 Month – 115 Years · Tout sèks · Mizajou Sep 22, 2026 · NCT00369421

Human Biospecimen Procurement Protocol: Biorepository to Support Translational Research to Identify Disease Mechanism(s)

Ap rekriteEtid obsèvasyonVolontè an sante akeyi
1 Month – 100 Years · Tout sèks · Mizajou Sep 22, 2026 · NCT02543996

A First-in-human Study of KK8123 in Adults With X-linked Hypophosphatemia

Ap rekriteFaz 1/2
Laj 18 a 65 · Tout sèks · Mizajou Sep 21, 2026 · NCT06525636

Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network

Ap rekriteEtid obsèvasyonVolontè an sante akeyi
1 Month – 100 Years · Tout sèks · Mizajou Sep 18, 2026 · NCT02450851

Caregiving Networks Across Disease Context and the Life Course

Ap rekriteEtid obsèvasyonVolontè an sante akeyi
Laj 18 a 100 · Tout sèks · Mizajou Sep 15, 2026 · NCT05007990

Longitudinal Studies of Patient With FPDMM

Ap rekriteEtid obsèvasyonVolontè an sante akeyi
1 Day – 100 Years · Tout sèks · Mizajou Sep 11, 2026 · NCT03854318

Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study

Ap rekriteEtid obsèvasyonVolontè an sante akeyi
Tout laj · Tout sèks · Mizajou Sep 1, 2026 · NCT06016946

Elafibranor Pregnancy Surveillance Program: A Study to Evaluate the Safety of Elafibranor During Pregnancy

Ap rekriteEtid obsèvasyon
Tout laj · Fanm · Mizajou Aug 31, 2026 · NCT07556913

International Rare Brain Tumor Registry

Ap rekriteEtid obsèvasyon
Jiska laj 45 · Tout sèks · Mizajou Aug 7, 2026 · NCT05697874

Stakeholders of Rare Diseases Informing Values In Neuroethics

Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Jul 13, 2026 · NCT07314736

Evaluation of an Advanced Lower Extremity Neuroprostheses

Ap rekrite
Laj 21 a 75 · Tout sèks · Mizajou Jul 10, 2026 · NCT00623389

A Study Evaluating the Real-World Experience of Givinostat in Patients With Duchenne Muscular Dystrophy

Ap rekriteEtid obsèvasyon
Laj 6 ak plis · Tout sèks · Mizajou Jul 2, 2026 · NCT07127978

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

Ap rekriteFaz 2
Laj 18 ak plis · Tout sèks · Mizajou Jun 23, 2026 · NCT07123155

Baker Gordon Syndrome Natural History Study

Ap rekriteEtid obsèvasyon
Laj 0 a 99 · Tout sèks · Mizajou Jun 3, 2026 · NCT06399952

UW Undiagnosed Genetic Diseases Program

Ap rekriteEtid obsèvasyon
Jiska laj 100 · Tout sèks · Mizajou May 29, 2026 · NCT04586075

Direct to Patient Minimal Risk Biospecimen and Data Collection Research

Ap rekriteEtid obsèvasyonVolontè an sante akeyi
Laj 18 a 90 · Tout sèks · Mizajou May 5, 2026 · NCT07128966

A Randomized Study of SPK-10001 Gene Therapy in Participants With Huntington's Disease

Ap rekriteFaz 1/2
Laj 25 a 65 · Tout sèks · Mizajou May 5, 2026 · NCT06826612

A Study of AAV9 Gene Therapy in Participants With Canavan Disease (CANaspire Clinical Trial)

Ap rekriteFaz 1/2
30 Months · Tout sèks · Mizajou Apr 17, 2026 · NCT04998396

Gene Discovery Core, The Manton Center

Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Mar 25, 2026 · NCT02743845

Delineating the Molecular Spectrum and the Clinical, Imaging and Neuronal Phenotype of Chopra-Amiel-Gordon Syndrome

Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Feb 17, 2026 · NCT05528744

MIHRA - Patient-Rooted Insights for Shaping Myositis Science (PRISMS)

Ap rekriteEtid obsèvasyon
Laj 7 ak plis · Tout sèks · Mizajou Jan 28, 2026 · NCT07374107

Genetic Study to Determine the Cause of Birth Defects in Newborns in Texas

Ap rekriteVolontè an sante akeyi
1 Day – 90 Days · Tout sèks · Mizajou Jan 27, 2026 · NCT07102966

Sous ClinicalTrials.gov, done yo ranmase Oct 1, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.