Akèy › Atrofi miskilè spinal › North Carolina
Etid klinik pou Atrofi miskilè spinal nan North Carolina
3 etid pou Atrofi miskilè spinal ap chèche patisipan nan sit nan North Carolina.
Vil nan North Carolina
Tèks ofisyèl etid la (Anglè)
A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Rare Disease Research NC, LLC, Hillsborough
Ap rekriteFaz 2
Laj 5 a 17 · Tout sèks · Mizajou Sep 14, 2026 · NCT07287982Clinical Procedures to Support Research in ALS
- Duke University, Durham
- Wake Forest University, Winston-Salem
Ap rekriteEtid obsèvasyon
Laj 18 ak plis · Tout sèks · Mizajou Jun 15, 2026 · NCT03489278Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
- Duke Health, Durham
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Jan 31, 2025 · NCT04174157Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.