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Uji klinis Ataksia Friedreich di Pennsylvania
4 studi untuk Ataksia Friedreich mencari peserta di lokasi di Pennsylvania.
Kota di Pennsylvania
Teks studi resmi (Bahasa Inggris)
A Study of SGT-212 Gene Therapy in Friedreich's Ataxia
- The Children's Hospital of Philadelphia (CHOP), Philadelphia
Menerima pesertaFase 1
Usia 18 hingga 40 · Semua jenis kelamin · Diperbarui 29 Sep 2026 · NCT07180355An Open-Label Study of CTI-1601 in Subjects With Friedreich's Ataxia
- Children's Hospital of the University of Pennsylvania (CHOP), Philadelphia
Menerima pesertaFase 2
Usia 2 hingga 60 · Semua jenis kelamin · Diperbarui 3 Sep 2026 · NCT06447025Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study
- Children's Hospital of Philadelphia, Philadelphia
Menerima pesertaStudi observasionalSukarelawan sehat diterima
Semua usia · Semua jenis kelamin · Diperbarui 1 Sep 2026 · NCT06016946A Study to Learn More About the Long-Term Safety of BIIB141 (Omaveloxolone) in Participants With Friedreich's Ataxia Who Are Prescribed it by Their Own Doctors
- Children's Hospital of Philadelphia, Philadelphia
Menerima pesertaStudi observasional
Usia 16 ke atas · Semua jenis kelamin · Diperbarui 28 Apr 2026 · NCT06623890Dari ClinicalTrials.gov, data diambil 5 Okt 2026. Setiap studi menetapkan kriteria kelayakannya sendiri; tim studi yang menentukan siapa yang bisa bergabung.