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Beranda › Kelainan Genetik › Florida

Uji klinis Kelainan Genetik di Florida

7 studi untuk Kelainan Genetik mencari peserta di lokasi di Florida.

Kota di Florida

Teks studi resmi (Bahasa Inggris)

Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network

  • University of Miami Miller School of Medicine, Miami
Menerima pesertaStudi observasionalSukarelawan sehat diterima
1 Month – 100 Years · Semua jenis kelamin · Diperbarui 2 Okt 2026 · NCT02450851

Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study

  • University of Florida - Neurology, Gainesville
  • USF Ataxia Research Center, Tampa
Menerima pesertaStudi observasionalSukarelawan sehat diterima
Semua usia · Semua jenis kelamin · Diperbarui 1 Sep 2026 · NCT06016946

A Non-inferiority Pharmacokinetic and Safety/Tolerability Study of Two Different Doses of Weekly SC Alpha1-PI 15% Compared With Corresponding Standard IV Alpha1-PI in Participants With Alpha1-Antitrypsin Deficiency (AATD)

  • GC2501 Study Site 103, Gainesville
  • GC2501 Study Site 105, Miami
Menerima pesertaFase 3
Usia 18 hingga 80 · Semua jenis kelamin · Diperbarui 11 Agu 2026 · NCT07555483

Safety of Anumigilimab (CSL324) in Adults With Sickle Cell Disease (SCD)

  • The Foundation for Sickle Cell Disease, Hollywood
Menerima pesertaFase 2
Usia 18 ke atas · Semua jenis kelamin · Diperbarui 5 Agu 2026 · NCT07224360

Rett Syndrome Registry

  • Nicklaus Children's Hospital, Miami
Menerima pesertaStudi observasional
Usia 0 hingga 99 · Semua jenis kelamin · Diperbarui 30 Jun 2026 · NCT05432349

A Study Investigating the Effectiveness and Safety of Garadacimab for Treating Patients With Hereditary Angioedema (HAE)

  • Sirven and Associates, Miami
Menerima pesertaStudi observasional
Usia 12 ke atas · Semua jenis kelamin · Diperbarui 3 Jun 2026 · NCT07001280

Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia

  • Nicklaus Children's Hospital, Miami
  • University of South Florida - 12901 Bruce B Downs, Tampa
Menerima pesertaFase 1/2
Semua usia · Semua jenis kelamin · Diperbarui 22 Jan 2026 · NCT04159103

Dari ClinicalTrials.gov, data diambil 3 Okt 2026. Setiap studi menetapkan kriteria kelayakannya sendiri; tim studi yang menentukan siapa yang bisa bergabung.