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Uji klinis Leukoensefalopati di Pennsylvania

4 studi untuk Leukoensefalopati mencari peserta di lokasi di Pennsylvania.

Kota di Pennsylvania

Teks studi resmi (Bahasa Inggris)

An Open-Label Exploratory Study of Fosigotifator in Participants With Vanishing White Matter Disease

  • Children's Hospital of Philadelphia, Philadelphia
Menerima pesertaFase 1/2
6 Months · Semua jenis kelamin · Diperbarui 24 Sep 2026 · NCT05757141

Longitudinal Study of Neurodegenerative Disorders

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Menerima pesertaStudi observasional
Semua usia · Semua jenis kelamin · Diperbarui 9 Feb 2026 · NCT03333200

North American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC)

  • The Children's Hospital of Philadelphia, Philadelphia
  • Children's Hospital of Pittsburgh, Pittsburgh
Menerima pesertaStudi observasionalSukarelawan sehat diterima
Semua usia · Semua jenis kelamin · Diperbarui 4 Feb 2026 · NCT01694940

The Myelin Disorders Biorepository Project

  • The Children's Hospital of Philadelphia, Philadelphia
  • University of Pennsylvania, Philadelphia
  • University of Pittsburgh Medical Center, Pittsburgh
Menerima pesertaStudi observasional
Semua usia · Semua jenis kelamin · Diperbarui 23 Okt 2025 · NCT03047369

Dari ClinicalTrials.gov, data diambil 5 Okt 2026. Setiap studi menetapkan kriteria kelayakannya sendiri; tim studi yang menentukan siapa yang bisa bergabung.