🔎 Trials Near Me

Beranda › Penyakit Langka › California

Uji klinis Penyakit Langka di California

10 studi untuk Penyakit Langka mencari peserta di lokasi di California.

Kota di California

Teks studi resmi (Bahasa Inggris)

Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network

  • University of California, Los Angeles, Los Angeles
  • University of California, Irvine Medical Center, Orange
  • Stanford University, Stanford
  • dan 2 lainnya
Menerima pesertaStudi observasionalSukarelawan sehat diterima
1 Month – 100 Years · Semua jenis kelamin · Diperbarui 2 Okt 2026 · NCT02450851

A Study of SGT-212 Gene Therapy in Friedreich's Ataxia

  • The University of California, Los Angeles (UCLA), Los Angeles
Menerima pesertaFase 1
Usia 18 hingga 40 · Semua jenis kelamin · Diperbarui 29 Sep 2026 · NCT07180355

A First-in-human Study of KK8123 in Adults With X-linked Hypophosphatemia

  • University of California - San Francisco, San Francisco
Menerima pesertaFase 1/2
Usia 18 hingga 65 · Semua jenis kelamin · Diperbarui 21 Sep 2026 · NCT06525636

Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study

  • UCLA Ataxia Center, Los Angeles
Menerima pesertaStudi observasionalSukarelawan sehat diterima
Semua usia · Semua jenis kelamin · Diperbarui 1 Sep 2026 · NCT06016946

International Rare Brain Tumor Registry

  • Children's Hospital Los Angeles, Los Angeles
  • University of California San Francisco, San Francisco
Menerima pesertaStudi observasional
Hingga usia 45 · Semua jenis kelamin · Diperbarui 7 Agu 2026 · NCT05697874

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

  • University of California - Irvine Medical Center, Irvine
Menerima pesertaFase 2
Usia 18 ke atas · Semua jenis kelamin · Diperbarui 23 Jun 2026 · NCT07123155

A Study of AAV9 Gene Therapy in Participants With Canavan Disease (CANaspire Clinical Trial)

  • UCSF Benioff Children's Hospital Oakland, Oakland
Menerima pesertaFase 1/2
30 Months · Semua jenis kelamin · Diperbarui 17 Apr 2026 · NCT04998396

The ExTINGUISH Trial of Inebilizumab in NMDAR Encephalitis

  • Children's Hospital of Orange County, Orange
  • UC Irvine, Orange
  • UC Davis, Sacramento
Menerima pesertaFase 2
Usia 12 ke atas · Semua jenis kelamin · Diperbarui 1 Jul 2025 · NCT04372615

Prospective Observational International Registry of Patients With Newly Diagnosed Peripheral T Cell Lymphoma.

  • Stanford University, Stanford
Menerima pesertaStudi observasional
Usia 18 ke atas · Semua jenis kelamin · Diperbarui 6 Mei 2025 · NCT03964480

Epilepsy Learning Healthcare System (ELHS)

  • Children's Hospital Los Angeles, Los Angeles
  • University of Southern California, Los Angeles
Menerima pesertaStudi observasional
Semua usia · Semua jenis kelamin · Diperbarui 30 Agu 2024 · NCT06265103

Dari ClinicalTrials.gov, data diambil 5 Okt 2026. Setiap studi menetapkan kriteria kelayakannya sendiri; tim studi yang menentukan siapa yang bisa bergabung.