Beranda › Penyakit Sel Sabit › Massachusetts
Uji klinis Penyakit Sel Sabit di Massachusetts
10 studi untuk Penyakit Sel Sabit mencari peserta di lokasi di Massachusetts.
Kota di Massachusetts
Teks studi resmi (Bahasa Inggris)
A Study to Evaluate How Well Etavopivat Works in People With Sickle Cell Disease
- Boston Children's Hospital, Boston
- Boston Medical Center, Boston
Menerima pesertaFase 3
Usia 12 ke atas · Semua jenis kelamin · Diperbarui 17 Sep 2026 · NCT06612268A Phase I/II Study of ITU512 in Healthy Participants and Patients With Sickle Cell Disease
- Boston Childrens Hospital, Boston
Menerima pesertaFase 1/2Sukarelawan sehat diterima
Usia 12 hingga 55 · Semua jenis kelamin · Diperbarui 9 Sep 2026 · NCT06546670A Study to Evaluate BMS-986470 in Healthy Volunteers and Participants With Sickle Cell Disease
- Local Institution - 0024, Boston
- Boston Medical Center, Boston
Menerima pesertaFase 1/2Sukarelawan sehat diterima
Usia 18 ke atas · Semua jenis kelamin · Diperbarui 18 Agu 2026 · NCT06481306ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders
- Massachusetts General Hospital Comprehensive Hemophilia and Thrombosis Treatment Center, Boston
Menerima pesertaStudi observasional
Semua usia · Semua jenis kelamin · Diperbarui 17 Agu 2026 · NCT04398628Comparing the Effectiveness of Matched Related Donor Hematopoietic Stem Cell Transplantation to Disease Modifying Therapy in Pediatric Patients With Sickle Cell Disease
- Boston Children's Hospital (MRD-HCT), Boston
- Boston Children's Hospital (NT-DMT), Boston
Menerima pesertaStudi observasional
Usia 3 hingga 20 · Semua jenis kelamin · Diperbarui 4 Jun 2026 · NCT06941389Promoting Resilience Among Adolescents and Young Adults With Sickle Cell Disease
- Boston Children's Hospital, Boston
Menerima peserta
Usia 8 hingga 25 · Semua jenis kelamin · Diperbarui 5 Mei 2026 · NCT06555939Hematopoietic Stem Cell BCL11A Enhancer Gene Editing for Severe β-Hemoglobinopathies
- Boston Children's Hospital, Boston
Menerima pesertaFase 1
Usia 13 hingga 40 · Semua jenis kelamin · Diperbarui 3 Feb 2026 · NCT06647979A Long-term Follow-up Study in Patients Who Received BEAM-101
- Boston Children's Hospital, Boston
Menerima pesertaStudi observasional
Usia 14 hingga 37 · Semua jenis kelamin · Diperbarui 28 Jan 2026 · NCT07373639A Pilot Study on Neuroimaging in SCD: Part of The Boston Consortium to Cure Sickle Cell Disease
- Boston Children's Hospital, Boston
Menerima pesertaStudi observasional
Usia 8 hingga 18 · Semua jenis kelamin · Diperbarui 12 Des 2025 · NCT04166526Study of the Role of Genetic Modifiers in Hemoglobinopathies
- Boston Children's Hospital, Boston
Menerima pesertaStudi observasional
Usia 2 ke atas · Semua jenis kelamin · Diperbarui 20 Mar 2024 · NCT05799118Dari ClinicalTrials.gov, data diambil 5 Okt 2026. Setiap studi menetapkan kriteria kelayakannya sendiri; tim studi yang menentukan siapa yang bisa bergabung.