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Uji klinis Atrofi Otot Tulang Belakang di California

11 studi untuk Atrofi Otot Tulang Belakang mencari peserta di lokasi di California.

Kota di California

Teks studi resmi (Bahasa Inggris)

A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy

  • Children's Hospital of Orange County (CHOC), Orange
  • Stanford Neuroscience Health Center (SNHC), Palo Alto
Menerima pesertaFase 2
Hingga usia 2 · Semua jenis kelamin · Diperbarui 2 Okt 2026 · NCT07047144

A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy

  • Stanford University Medical Center, Stanford
Menerima pesertaFase 2
Usia 5 hingga 17 · Semua jenis kelamin · Diperbarui 14 Sep 2026 · NCT07287982

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy

  • Valley Children's Hospital, Madera
  • Stanford Univ Medical Center, Palo Alto
Menerima pesertaFase 4
3 Months – 24 Months · Semua jenis kelamin · Diperbarui 10 Sep 2026 · NCT05861999

A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)

  • Children's Hospital of Orange County, Orange
  • Stanford University Medical Center | Department of Neurology_Palo Alto, Palo Alto
Menerima pesertaFase 1
Usia 3 ke atas · Semua jenis kelamin · Diperbarui 3 Sep 2026 · NCT06555419

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

  • Children's Hospital Orange County, Orange
  • Stanford Medical Center, Palo Alto
  • Rady Children's Hospital, San Diego
Menerima peserta
Usia 3 ke atas · Semua jenis kelamin · Diperbarui 19 Agu 2026 · NCT05866419

Clinical Procedures to Support Research in ALS

  • University of California, Irvine, Irvine
  • Stanford University, Palo Alto
  • California Pacific Medical Center, San Francisco
Menerima pesertaStudi observasional
Usia 18 ke atas · Semua jenis kelamin · Diperbarui 15 Jun 2026 · NCT03489278

ALS/MND Natural History Study Data Repository

  • Loma Linda University Health, Loma Linda
  • Kaiser Permanente, Los Angeles
Menerima pesertaStudi observasional
Usia 18 hingga 90 · Semua jenis kelamin · Diperbarui 20 Mei 2026 · NCT05966038

Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders

  • Stanford University, Palo Alto
Menerima pesertaStudi observasionalSukarelawan sehat diterima
Usia 5 ke atas · Semua jenis kelamin · Diperbarui 9 Apr 2026 · NCT06839469

A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies

  • Stanford Neuroscience Health Center, Palo Alto
Menerima pesertaStudi observasional
Usia 18 hingga 54 · Wanita · Diperbarui 9 Mar 2026 · NCT05789758

Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

  • Children's Hospital of Los Angeles, Los Angeles
  • University of California Los Angeles Health, Los Angeles
  • Valley Children's Healthcare, Madera
  • dan 3 lainnya
Menerima pesertaStudi observasional
Semua usia · Semua jenis kelamin · Diperbarui 31 Jan 2025 · NCT04174157

Dari ClinicalTrials.gov, data diambil 6 Okt 2026. Setiap studi menetapkan kriteria kelayakannya sendiri; tim studi yang menentukan siapa yang bisa bergabung.