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Uji klinis Atrofi Otot Tulang Belakang di California
11 studi untuk Atrofi Otot Tulang Belakang mencari peserta di lokasi di California.
Kota di California
Teks studi resmi (Bahasa Inggris)
A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety in Participants Aged 15 to 60 Years With Spinal Muscular Atrophy (SMA) Who Are Either New to SMA Treatment or Were Previously Treated With Risdiplam
- Stanford University Medical Center, Palo Alto
Menerima pesertaFase 3
Usia 15 hingga 60 · Semua jenis kelamin · Diperbarui 2 Okt 2026 · NCT07444476A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy
- Children's Hospital of Orange County (CHOC), Orange
- Stanford Neuroscience Health Center (SNHC), Palo Alto
Menerima pesertaFase 2
Hingga usia 2 · Semua jenis kelamin · Diperbarui 2 Okt 2026 · NCT07047144A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Stanford University Medical Center, Stanford
Menerima pesertaFase 2
Usia 5 hingga 17 · Semua jenis kelamin · Diperbarui 14 Sep 2026 · NCT07287982A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
- Valley Children's Hospital, Madera
- Stanford Univ Medical Center, Palo Alto
Menerima pesertaFase 4
3 Months – 24 Months · Semua jenis kelamin · Diperbarui 10 Sep 2026 · NCT05861999A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)
- Children's Hospital of Orange County, Orange
- Stanford University Medical Center | Department of Neurology_Palo Alto, Palo Alto
Menerima pesertaFase 1
Usia 3 ke atas · Semua jenis kelamin · Diperbarui 3 Sep 2026 · NCT06555419Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
- Children's Hospital Orange County, Orange
- Stanford Medical Center, Palo Alto
- Rady Children's Hospital, San Diego
Menerima peserta
Usia 3 ke atas · Semua jenis kelamin · Diperbarui 19 Agu 2026 · NCT05866419Clinical Procedures to Support Research in ALS
- University of California, Irvine, Irvine
- Stanford University, Palo Alto
- California Pacific Medical Center, San Francisco
Menerima pesertaStudi observasional
Usia 18 ke atas · Semua jenis kelamin · Diperbarui 15 Jun 2026 · NCT03489278ALS/MND Natural History Study Data Repository
- Loma Linda University Health, Loma Linda
- Kaiser Permanente, Los Angeles
Menerima pesertaStudi observasional
Usia 18 hingga 90 · Semua jenis kelamin · Diperbarui 20 Mei 2026 · NCT05966038Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders
- Stanford University, Palo Alto
Menerima pesertaStudi observasionalSukarelawan sehat diterima
Usia 5 ke atas · Semua jenis kelamin · Diperbarui 9 Apr 2026 · NCT06839469A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies
- Stanford Neuroscience Health Center, Palo Alto
Menerima pesertaStudi observasional
Usia 18 hingga 54 · Wanita · Diperbarui 9 Mar 2026 · NCT05789758Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
- Children's Hospital of Los Angeles, Los Angeles
- University of California Los Angeles Health, Los Angeles
- Valley Children's Healthcare, Madera
- dan 3 lainnya
Menerima pesertaStudi observasional
Semua usia · Semua jenis kelamin · Diperbarui 31 Jan 2025 · NCT04174157Dari ClinicalTrials.gov, data diambil 6 Okt 2026. Setiap studi menetapkan kriteria kelayakannya sendiri; tim studi yang menentukan siapa yang bisa bergabung.