フロリダ州における脊髄性筋萎縮症の臨床試験
フロリダ州内の拠点で、脊髄性筋萎縮症に関する8件の研究が参加者を募集しています。
フロリダ州内の都市
公式研究テキスト（英語）
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
- University of Florida Pediatrics, Gainesville
被験者募集中第4相
3 Months – 24 Months · 全性別 · 2026/10/02更新 · NCT05861986A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Rare Disease Research FL LLC, Kissimmee
被験者募集中第2相
5歳〜17歳 · 全性別 · 2026/09/14更新 · NCT07287982A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
- University of Florida Pediatrics, Gainesville
被験者募集中第4相
3 Months – 24 Months · 全性別 · 2026/09/10更新 · NCT05861999A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)
- Nemours Children's Hospital, Orlando, Orlando
被験者募集中第1相
3歳以上 · 全性別 · 2026/09/03更新 · NCT06555419Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
- Nemours Children's Hospital, Florida, Orlando
被験者募集中
3歳以上 · 全性別 · 2026/08/19更新 · NCT05866419Clinical Procedures to Support Research in ALS
- University of Miami, Miami
被験者募集中観察研究
18歳以上 · 全性別 · 2026/06/15更新 · NCT03489278ALS/MND Natural History Study Data Repository
- University of Florida, Gainesville
被験者募集中観察研究
18歳〜90歳 · 全性別 · 2026/05/20更新 · NCT05966038Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
- Golisano Children's Hospital of Southwest Florida, Fort Myers
- Jackson South Medical Center, Palmetto Bay
被験者募集中観察研究
全年齢 · 全性別 · 2025/01/31更新 · NCT04174157ClinicalTrials.govより、2026/10/05時点のデータを取得。各研究には独自の参加資格があり、参加可否は研究チームが決定します。