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Friedreich Ataxia clinical trials in California

5 studies for Friedreich Ataxia are looking for participants at sites in California.

Cities in California

A Study of SGT-212 Gene Therapy in Friedreich's Ataxia

  • The University of California, Los Angeles (UCLA), Los Angeles
RecruitingPhase 1
Ages 18 to 40 · All sexes · Updated Sep 29, 2026 · NCT07180355

An Open-Label Study of CTI-1601 in Subjects With Friedreich's Ataxia

  • University of California Los Angeles, Los Angeles
RecruitingPhase 2
Ages 2 to 60 · All sexes · Updated Sep 3, 2026 · NCT06447025

Clinical Course Of Disease In Participants With FA-CM

  • University of California San Diego, La Jolla
RecruitingObservational study
Ages 6 and older · All sexes · Updated Sep 2, 2026 · NCT06865482

Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study

  • UCLA Ataxia Center, Los Angeles
RecruitingObservational studyHealthy volunteers welcome
All ages · All sexes · Updated Sep 1, 2026 · NCT06016946

A Study to Learn More About the Long-Term Safety of BIIB141 (Omaveloxolone) in Participants With Friedreich's Ataxia Who Are Prescribed it by Their Own Doctors

  • UCLA Neurology, Los Angeles
RecruitingObservational study
Ages 16 and older · All sexes · Updated Apr 28, 2026 · NCT06623890

From ClinicalTrials.gov, data retrieved Oct 5, 2026. Each study sets its own eligibility; the study team decides who can join.