Pradžia › Genetiniai sutrikimai › Florida
Genetiniai sutrikimai klinikiniai tyrimai Florida
7 tyrimai dėl Genetiniai sutrikimai ieško dalyvių vietose Florida.
Miestai Florida
Oficialus tyrimo tekstas (anglų kalba)
Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network
- University of Miami Miller School of Medicine, Miami
Renkami dalyviaiStebimasis tyrimasLaukiami sveiki savanoriai
1 Month – 100 Years · Visoms lytims · Atnaujinta 2026-10-02 · NCT02450851Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study
- University of Florida - Neurology, Gainesville
- USF Ataxia Research Center, Tampa
Renkami dalyviaiStebimasis tyrimasLaukiami sveiki savanoriai
Visi amžiai · Visoms lytims · Atnaujinta 2026-09-01 · NCT06016946A Non-inferiority Pharmacokinetic and Safety/Tolerability Study of Two Different Doses of Weekly SC Alpha1-PI 15% Compared With Corresponding Standard IV Alpha1-PI in Participants With Alpha1-Antitrypsin Deficiency (AATD)
- GC2501 Study Site 103, Gainesville
- GC2501 Study Site 105, Miami
Renkami dalyviai3 fazė
Amžius nuo 18 iki 80 · Visoms lytims · Atnaujinta 2026-08-11 · NCT07555483Safety of Anumigilimab (CSL324) in Adults With Sickle Cell Disease (SCD)
- The Foundation for Sickle Cell Disease, Hollywood
Renkami dalyviai2 fazė
Amžius 18 ir vyresni · Visoms lytims · Atnaujinta 2026-08-05 · NCT07224360Rett Syndrome Registry
- Nicklaus Children's Hospital, Miami
Renkami dalyviaiStebimasis tyrimas
Amžius nuo 0 iki 99 · Visoms lytims · Atnaujinta 2026-06-30 · NCT05432349A Study Investigating the Effectiveness and Safety of Garadacimab for Treating Patients With Hereditary Angioedema (HAE)
- Sirven and Associates, Miami
Renkami dalyviaiStebimasis tyrimas
Amžius 12 ir vyresni · Visoms lytims · Atnaujinta 2026-06-03 · NCT07001280Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia
- Nicklaus Children's Hospital, Miami
- University of South Florida - 12901 Bruce B Downs, Tampa
Renkami dalyviai1/2 fazė
Visi amžiai · Visoms lytims · Atnaujinta 2026-01-22 · NCT04159103Iš ClinicalTrials.gov, duomenys gauti 2026-10-04. Kiekvienas tyrimas nustato savo tinkamumo kriterijus; tyrimo komanda sprendžia, kas gali dalyvauti.