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Genetiniai sutrikimai klinikiniai tyrimai Florida

7 tyrimai dėl Genetiniai sutrikimai ieško dalyvių vietose Florida.

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Oficialus tyrimo tekstas (anglų kalba)

Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network

  • University of Miami Miller School of Medicine, Miami
Renkami dalyviaiStebimasis tyrimasLaukiami sveiki savanoriai
1 Month – 100 Years · Visoms lytims · Atnaujinta 2026-10-02 · NCT02450851

Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study

  • University of Florida - Neurology, Gainesville
  • USF Ataxia Research Center, Tampa
Renkami dalyviaiStebimasis tyrimasLaukiami sveiki savanoriai
Visi amžiai · Visoms lytims · Atnaujinta 2026-09-01 · NCT06016946

A Non-inferiority Pharmacokinetic and Safety/Tolerability Study of Two Different Doses of Weekly SC Alpha1-PI 15% Compared With Corresponding Standard IV Alpha1-PI in Participants With Alpha1-Antitrypsin Deficiency (AATD)

  • GC2501 Study Site 103, Gainesville
  • GC2501 Study Site 105, Miami
Renkami dalyviai3 fazė
Amžius nuo 18 iki 80 · Visoms lytims · Atnaujinta 2026-08-11 · NCT07555483

Safety of Anumigilimab (CSL324) in Adults With Sickle Cell Disease (SCD)

  • The Foundation for Sickle Cell Disease, Hollywood
Renkami dalyviai2 fazė
Amžius 18 ir vyresni · Visoms lytims · Atnaujinta 2026-08-05 · NCT07224360

Rett Syndrome Registry

  • Nicklaus Children's Hospital, Miami
Renkami dalyviaiStebimasis tyrimas
Amžius nuo 0 iki 99 · Visoms lytims · Atnaujinta 2026-06-30 · NCT05432349

A Study Investigating the Effectiveness and Safety of Garadacimab for Treating Patients With Hereditary Angioedema (HAE)

  • Sirven and Associates, Miami
Renkami dalyviaiStebimasis tyrimas
Amžius 12 ir vyresni · Visoms lytims · Atnaujinta 2026-06-03 · NCT07001280

Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia

  • Nicklaus Children's Hospital, Miami
  • University of South Florida - 12901 Bruce B Downs, Tampa
Renkami dalyviai1/2 fazė
Visi amžiai · Visoms lytims · Atnaujinta 2026-01-22 · NCT04159103

Iš ClinicalTrials.gov, duomenys gauti 2026-10-04. Kiekvienas tyrimas nustato savo tinkamumo kriterijus; tyrimo komanda sprendžia, kas gali dalyvauti.