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Genetiniai sutrikimai klinikiniai tyrimai Ohio
7 tyrimai dėl Genetiniai sutrikimai ieško dalyvių vietose Ohio.
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Oficialus tyrimo tekstas (anglų kalba)
Study to Evaluate the Efficacy and Safety of BMN 333 Versus Vosoritide in Children With Achondroplasia
- Cincinnati Children's Hospital Medical Center, Cincinnati
Renkami dalyviai2/3 fazė
Amžius nuo 2 iki 17 · Visoms lytims · Atnaujinta 2026-09-24 · NCT07441876Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study
- Ohio State University - Neurology, Columbus
Renkami dalyviaiStebimasis tyrimasLaukiami sveiki savanoriai
Visi amžiai · Visoms lytims · Atnaujinta 2026-09-01 · NCT06016946A Non-inferiority Pharmacokinetic and Safety/Tolerability Study of Two Different Doses of Weekly SC Alpha1-PI 15% Compared With Corresponding Standard IV Alpha1-PI in Participants With Alpha1-Antitrypsin Deficiency (AATD)
- GC2501 Study Site 104, Cleveland
Renkami dalyviai3 fazė
Amžius nuo 18 iki 80 · Visoms lytims · Atnaujinta 2026-08-11 · NCT07555483Safety of Anumigilimab (CSL324) in Adults With Sickle Cell Disease (SCD)
- Ohio State University, Columbus
Renkami dalyviai2 fazė
Amžius 18 ir vyresni · Visoms lytims · Atnaujinta 2026-08-05 · NCT07224360Prospective Clinical Assessment Study in Children With Hypochondroplasia
- Cincinnati Children's Hospital Medical Center, Cincinnati
Renkami dalyviaiStebimasis tyrimas
30 Months – 16 Years · Visoms lytims · Atnaujinta 2026-07-16 · NCT06410976Rett Syndrome Registry
- Cincinnati Children's Hospital Medical Center, Cincinnati
- Nationwide Children's Hospital, Columbus
Renkami dalyviaiStebimasis tyrimas
Amžius nuo 0 iki 99 · Visoms lytims · Atnaujinta 2026-06-30 · NCT05432349Helix Research Network
- TriHealth (DNA Discovery), Cincinnati
- The Ohio State University (Genomic Health), Columbus
Renkami dalyviaiStebimasis tyrimasLaukiami sveiki savanoriai
Amžius 18 ir vyresni · Visoms lytims · Atnaujinta 2026-03-23 · NCT06057181Iš ClinicalTrials.gov, duomenys gauti 2026-10-05. Kiekvienas tyrimas nustato savo tinkamumo kriterijus; tyrimo komanda sprendžia, kas gali dalyvauti.