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Genetiniai sutrikimai klinikiniai tyrimai Tennessee

5 tyrimai dėl Genetiniai sutrikimai ieško dalyvių vietose Tennessee.

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Oficialus tyrimo tekstas (anglų kalba)

Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network

  • Vanderbilt University Medical Center, Nashville
Renkami dalyviaiStebimasis tyrimasLaukiami sveiki savanoriai
1 Month – 100 Years · Visoms lytims · Atnaujinta 2026-10-02 · NCT02450851

Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study

  • St. Jude Children's Research Hospital, Memphis
Renkami dalyviaiStebimasis tyrimasLaukiami sveiki savanoriai
Visi amžiai · Visoms lytims · Atnaujinta 2026-09-01 · NCT06016946

Prospective Clinical Assessment Study in Children With Hypochondroplasia

  • Vanderbilt University Medical Center, Nashville
Renkami dalyviaiStebimasis tyrimas
30 Months – 16 Years · Visoms lytims · Atnaujinta 2026-07-16 · NCT06410976

Rett Syndrome Registry

  • Vanderbilt Kennedy Center, Nashville
Renkami dalyviaiStebimasis tyrimas
Amžius nuo 0 iki 99 · Visoms lytims · Atnaujinta 2026-06-30 · NCT05432349

Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease

  • TriStar Medical Group Children's Specialists - Pediatric Oncology, Nashville
Renkami dalyviai3 fazė
Amžius nuo 12 iki 35 · Visoms lytims · Atnaujinta 2026-03-23 · NCT05477563

Iš ClinicalTrials.gov, duomenys gauti 2026-10-05. Kiekvienas tyrimas nustato savo tinkamumo kriterijus; tyrimo komanda sprendžia, kas gali dalyvauti.