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Leukoencefalopatijos klinikiniai tyrimai Pennsylvania
4 tyrimai dėl Leukoencefalopatijos ieško dalyvių vietose Pennsylvania.
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Oficialus tyrimo tekstas (anglų kalba)
An Open-Label Exploratory Study of Fosigotifator in Participants With Vanishing White Matter Disease
- Children's Hospital of Philadelphia, Philadelphia
Renkami dalyviai1/2 fazė
6 Months · Visoms lytims · Atnaujinta 2026-09-24 · NCT05757141Longitudinal Study of Neurodegenerative Disorders
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
Renkami dalyviaiStebimasis tyrimas
Visi amžiai · Visoms lytims · Atnaujinta 2026-02-09 · NCT03333200North American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC)
- The Children's Hospital of Philadelphia, Philadelphia
- Children's Hospital of Pittsburgh, Pittsburgh
Renkami dalyviaiStebimasis tyrimasLaukiami sveiki savanoriai
Visi amžiai · Visoms lytims · Atnaujinta 2026-02-04 · NCT01694940The Myelin Disorders Biorepository Project
- The Children's Hospital of Philadelphia, Philadelphia
- University of Pennsylvania, Philadelphia
- University of Pittsburgh Medical Center, Pittsburgh
Renkami dalyviaiStebimasis tyrimas
Visi amžiai · Visoms lytims · Atnaujinta 2025-10-23 · NCT03047369Iš ClinicalTrials.gov, duomenys gauti 2026-10-05. Kiekvienas tyrimas nustato savo tinkamumo kriterijus; tyrimo komanda sprendžia, kas gali dalyvauti.