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Retos ligos klinikiniai tyrimai Pennsylvania

7 tyrimai dėl Retos ligos ieško dalyvių vietose Pennsylvania.

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Oficialus tyrimo tekstas (anglų kalba)

Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network

  • University of Pennsylvania, Philadelphia
  • Children's Hospital of Philadelphia, Philadelphia
Renkami dalyviaiStebimasis tyrimasLaukiami sveiki savanoriai
1 Month – 100 Years · Visoms lytims · Atnaujinta 2026-10-02 · NCT02450851

A Study of SGT-212 Gene Therapy in Friedreich's Ataxia

  • The Children's Hospital of Philadelphia (CHOP), Philadelphia
Renkami dalyviai1 fazė
Amžius nuo 18 iki 40 · Visoms lytims · Atnaujinta 2026-09-29 · NCT07180355

Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study

  • Children's Hospital of Philadelphia, Philadelphia
Renkami dalyviaiStebimasis tyrimasLaukiami sveiki savanoriai
Visi amžiai · Visoms lytims · Atnaujinta 2026-09-01 · NCT06016946

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

  • University of Pennsylvania, Philadelphia
  • University of Pittsburgh School of Medicine, Pittsburgh
Renkami dalyviai2 fazė
Amžius 18 ir vyresni · Visoms lytims · Atnaujinta 2026-06-23 · NCT07123155

A Randomized Study of SPK-10001 Gene Therapy in Participants With Huntington's Disease

  • University of Pennsylvania, Philadelphia
  • University of Pittsburg, Pittsburgh
Renkami dalyviai1/2 fazė
Amžius nuo 25 iki 65 · Visoms lytims · Atnaujinta 2026-05-05 · NCT06826612

The ExTINGUISH Trial of Inebilizumab in NMDAR Encephalitis

  • University of Pennsylvania, Philadelphia
  • University of Pittsburgh, Pittsburgh
Renkami dalyviai2 fazė
Amžius 12 ir vyresni · Visoms lytims · Atnaujinta 2025-07-01 · NCT04372615

Epilepsy Learning Healthcare System (ELHS)

  • Penn State Hershey, Hershey
  • Children's Hospital of Philadelphia (CHOP), Philadelphia
Renkami dalyviaiStebimasis tyrimas
Visi amžiai · Visoms lytims · Atnaujinta 2024-08-30 · NCT06265103

Iš ClinicalTrials.gov, duomenys gauti 2026-10-05. Kiekvienas tyrimas nustato savo tinkamumo kriterijus; tyrimo komanda sprendžia, kas gali dalyvauti.