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Retos ligos klinikiniai tyrimai Pennsylvania
7 tyrimai dėl Retos ligos ieško dalyvių vietose Pennsylvania.
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Oficialus tyrimo tekstas (anglų kalba)
Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network
- University of Pennsylvania, Philadelphia
- Children's Hospital of Philadelphia, Philadelphia
Renkami dalyviaiStebimasis tyrimasLaukiami sveiki savanoriai
1 Month – 100 Years · Visoms lytims · Atnaujinta 2026-10-02 · NCT02450851A Study of SGT-212 Gene Therapy in Friedreich's Ataxia
- The Children's Hospital of Philadelphia (CHOP), Philadelphia
Renkami dalyviai1 fazė
Amžius nuo 18 iki 40 · Visoms lytims · Atnaujinta 2026-09-29 · NCT07180355Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study
- Children's Hospital of Philadelphia, Philadelphia
Renkami dalyviaiStebimasis tyrimasLaukiami sveiki savanoriai
Visi amžiai · Visoms lytims · Atnaujinta 2026-09-01 · NCT06016946Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)
- University of Pennsylvania, Philadelphia
- University of Pittsburgh School of Medicine, Pittsburgh
Renkami dalyviai2 fazė
Amžius 18 ir vyresni · Visoms lytims · Atnaujinta 2026-06-23 · NCT07123155A Randomized Study of SPK-10001 Gene Therapy in Participants With Huntington's Disease
- University of Pennsylvania, Philadelphia
- University of Pittsburg, Pittsburgh
Renkami dalyviai1/2 fazė
Amžius nuo 25 iki 65 · Visoms lytims · Atnaujinta 2026-05-05 · NCT06826612The ExTINGUISH Trial of Inebilizumab in NMDAR Encephalitis
- University of Pennsylvania, Philadelphia
- University of Pittsburgh, Pittsburgh
Renkami dalyviai2 fazė
Amžius 12 ir vyresni · Visoms lytims · Atnaujinta 2025-07-01 · NCT04372615Epilepsy Learning Healthcare System (ELHS)
- Penn State Hershey, Hershey
- Children's Hospital of Philadelphia (CHOP), Philadelphia
Renkami dalyviaiStebimasis tyrimas
Visi amžiai · Visoms lytims · Atnaujinta 2024-08-30 · NCT06265103Iš ClinicalTrials.gov, duomenys gauti 2026-10-05. Kiekvienas tyrimas nustato savo tinkamumo kriterijus; tyrimo komanda sprendžia, kas gali dalyvauti.