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A Study to Evaluate How Well Etavopivat Works in People With Sickle Cell Disease

  • Boston Children's Hospital, Boston
  • Boston Medical Center, Boston
Renkami dalyviai3 fazė
Amžius 12 ir vyresni · Visoms lytims · Atnaujinta 2026-09-17 · NCT06612268

A Phase I/II Study of ITU512 in Healthy Participants and Patients With Sickle Cell Disease

  • Boston Childrens Hospital, Boston
Renkami dalyviai1/2 fazėLaukiami sveiki savanoriai
Amžius nuo 12 iki 55 · Visoms lytims · Atnaujinta 2026-09-09 · NCT06546670

A Study to Evaluate BMS-986470 in Healthy Volunteers and Participants With Sickle Cell Disease

  • Local Institution - 0024, Boston
  • Boston Medical Center, Boston
Renkami dalyviai1/2 fazėLaukiami sveiki savanoriai
Amžius 18 ir vyresni · Visoms lytims · Atnaujinta 2026-08-18 · NCT06481306

ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders

  • Massachusetts General Hospital Comprehensive Hemophilia and Thrombosis Treatment Center, Boston
Renkami dalyviaiStebimasis tyrimas
Visi amžiai · Visoms lytims · Atnaujinta 2026-08-17 · NCT04398628

Comparing the Effectiveness of Matched Related Donor Hematopoietic Stem Cell Transplantation to Disease Modifying Therapy in Pediatric Patients With Sickle Cell Disease

  • Boston Children's Hospital (MRD-HCT), Boston
  • Boston Children's Hospital (NT-DMT), Boston
Renkami dalyviaiStebimasis tyrimas
Amžius nuo 3 iki 20 · Visoms lytims · Atnaujinta 2026-06-04 · NCT06941389

Promoting Resilience Among Adolescents and Young Adults With Sickle Cell Disease

  • Boston Children's Hospital, Boston
Renkami dalyviai
Amžius nuo 8 iki 25 · Visoms lytims · Atnaujinta 2026-05-05 · NCT06555939

Hematopoietic Stem Cell BCL11A Enhancer Gene Editing for Severe β-Hemoglobinopathies

  • Boston Children's Hospital, Boston
Renkami dalyviai1 fazė
Amžius nuo 13 iki 40 · Visoms lytims · Atnaujinta 2026-02-03 · NCT06647979

A Long-term Follow-up Study in Patients Who Received BEAM-101

  • Boston Children's Hospital, Boston
Renkami dalyviaiStebimasis tyrimas
Amžius nuo 14 iki 37 · Visoms lytims · Atnaujinta 2026-01-28 · NCT07373639

A Pilot Study on Neuroimaging in SCD: Part of The Boston Consortium to Cure Sickle Cell Disease

  • Boston Children's Hospital, Boston
Renkami dalyviaiStebimasis tyrimas
Amžius nuo 8 iki 18 · Visoms lytims · Atnaujinta 2025-12-12 · NCT04166526

Study of the Role of Genetic Modifiers in Hemoglobinopathies

  • Boston Children's Hospital, Boston
Renkami dalyviaiStebimasis tyrimas
Amžius 2 ir vyresni · Visoms lytims · Atnaujinta 2024-03-20 · NCT05799118

Iš ClinicalTrials.gov, duomenys gauti 2026-10-05. Kiekvienas tyrimas nustato savo tinkamumo kriterijus; tyrimo komanda sprendžia, kas gali dalyvauti.