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Oficialus tyrimo tekstas (anglų kalba)

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy

  • Children's Healthcare of Atlanta Center for Advanced Pediatrics, Atlanta
Renkami dalyviai4 fazė
3 Months – 24 Months · Visoms lytims · Atnaujinta 2026-10-02 · NCT05861986

A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy

  • Children's Healthcare of Atlanta, Atlanta
Renkami dalyviai2 fazė
Iki 2 metų · Visoms lytims · Atnaujinta 2026-10-02 · NCT07047144

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy

  • Children's Healthcare of Atlanta Center for Advanced Pediatrics, Atlanta
Renkami dalyviai4 fazė
3 Months – 24 Months · Visoms lytims · Atnaujinta 2026-09-10 · NCT05861999

Iš ClinicalTrials.gov, duomenys gauti 2026-10-05. Kiekvienas tyrimas nustato savo tinkamumo kriterijus; tyrimo komanda sprendžia, kas gali dalyvauti.