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Stuburo raumenų atrofija klinikiniai tyrimai JAV ieško dalyvių
23 tyrimai dėl Stuburo raumenų atrofija ieško dalyvių vietose visoje Jungtinėse Valstijose.
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Nesenai atnaujinti tyrimai
Oficialus tyrimo tekstas (anglų kalba)
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
Renkami dalyviai4 fazė
3 Months – 24 Months · Visoms lytims · Atnaujinta 2026-10-02 · NCT05861986A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy
Renkami dalyviai2 fazė
Iki 2 metų · Visoms lytims · Atnaujinta 2026-10-02 · NCT07047144A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety in Participants Aged 15 to 60 Years With Spinal Muscular Atrophy (SMA) Who Are Either New to SMA Treatment or Were Previously Treated With Risdiplam
Renkami dalyviai3 fazė
Amžius nuo 15 iki 60 · Visoms lytims · Atnaujinta 2026-10-02 · NCT07444476A Registry of Cases of Spinal Muscular Atrophy
Renkami dalyviaiStebimasis tyrimas
Visi amžiai · Visoms lytims · Atnaujinta 2026-09-30 · NCT07805278ASsessing The REAl-world Safety & Effectiveness of Spinal Muscular Atrophy Participants Treated With Intrathecal Onasemnogene Abeparvovec-brve (OAV101B) (ITVISMA®): A U.S. Pragmatic Multicenter Study (STREAM)
Renkami dalyviai4 fazė
Amžius nuo 2 iki 100 · Visoms lytims · Atnaujinta 2026-09-18 · NCT07448610A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
Renkami dalyviai2 fazė
Amžius nuo 5 iki 17 · Visoms lytims · Atnaujinta 2026-09-14 · NCT07287982A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
Renkami dalyviai4 fazė
3 Months – 24 Months · Visoms lytims · Atnaujinta 2026-09-10 · NCT05861999A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)
Renkami dalyviai1 fazė
Amžius 3 ir vyresni · Visoms lytims · Atnaujinta 2026-09-03 · NCT06555419Interfacing With NeuroTechnology to Expand Neural Throughput (INTENT)
Renkami dalyviai
Amžius nuo 18 iki 80 · Visoms lytims · Atnaujinta 2026-09-02 · NCT07521930Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
Renkami dalyviai
Amžius 3 ir vyresni · Visoms lytims · Atnaujinta 2026-08-19 · NCT05866419A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety When Given Before Symptoms Appear in Babies With Genetically Diagnosed Spinal Muscular Atrophy (SMA)
Renkami dalyviai3 fazė
0 Days – 42 Days · Visoms lytims · Atnaujinta 2026-08-18 · NCT07221669A Study to Learn About the Safety and Effects of Salanersen (BIIB115) When Given to Babies With Spinal Muscular Atrophy (SMA) Who Were Previously Treated With Onasemnogene Abeparvovec
Renkami dalyviai3 fazė
0 Days – 7 Months · Visoms lytims · Atnaujinta 2026-08-11 · NCT07444450Exploring the Physiologic, Pharmacodynamic, and Clinical Responses of Skeletal Muscle in Patients With Spinal Muscular Atrophy Treated With SMN-Directed Therapies
Renkami dalyviaiStebimasis tyrimas
Amžius nuo 5 iki 20 · Visoms lytims · Atnaujinta 2026-07-09 · NCT06532474Clinical Procedures to Support Research in ALS
Renkami dalyviaiStebimasis tyrimas
Amžius 18 ir vyresni · Visoms lytims · Atnaujinta 2026-06-15 · NCT03489278ALS/MND Natural History Study Data Repository
Renkami dalyviaiStebimasis tyrimas
Amžius nuo 18 iki 90 · Visoms lytims · Atnaujinta 2026-05-20 · NCT05966038Characterizing Perceived Physical Fatigability in Nusinersen-treated SMA
Renkami dalyviaiStebimasis tyrimas
Amžius 12 ir vyresni · Visoms lytims · Atnaujinta 2026-05-14 · NCT06955897Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders
Renkami dalyviaiStebimasis tyrimasLaukiami sveiki savanoriai
Amžius 5 ir vyresni · Visoms lytims · Atnaujinta 2026-04-09 · NCT06839469HABIT-ILE + FST in Children With SMA: Preliminary Effectiveness
Renkami dalyviai
Amžius nuo 5 iki 17 · Visoms lytims · Atnaujinta 2026-03-23 · NCT07488338Gait and Bone Health in SMA
Renkami dalyviaiStebimasis tyrimas
Amžius nuo 8 iki 50 · Visoms lytims · Atnaujinta 2026-03-18 · NCT07400198Effects of Whole-body Electrical Muscle Stimulation Exercise on Adults With Neuromuscular Disease
Renkami dalyviai
Amžius 18 ir vyresni · Visoms lytims · Atnaujinta 2026-03-17 · NCT07478172A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies
Renkami dalyviaiStebimasis tyrimas
Amžius nuo 18 iki 54 · Moterims · Atnaujinta 2026-03-09 · NCT05789758Diagnostic Journey, Patient Experience, and Disparities in the Treatment of Spinal Muscular Atrophy (SMA) in the MedStar Health System
Renkami dalyviaiStebimasis tyrimas
Amžius 18 ir vyresni · Visoms lytims · Atnaujinta 2026-01-16 · NCT07223489Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
Renkami dalyviaiStebimasis tyrimas
Visi amžiai · Visoms lytims · Atnaujinta 2025-01-31 · NCT04174157Iš ClinicalTrials.gov, duomenys gauti 2026-10-05. Kiekvienas tyrimas nustato savo tinkamumo kriterijus; tyrimo komanda sprendžia, kas gali dalyvauti.