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Stuburo raumenų atrofija klinikiniai tyrimai Ilinoisas

6 tyrimai dėl Stuburo raumenų atrofija ieško dalyvių vietose Ilinoisas.

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Oficialus tyrimo tekstas (anglų kalba)

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy

  • Ann and Robert H. Lurie Children Hospital of Chicago, Chicago
Renkami dalyviai4 fazė
3 Months – 24 Months · Visoms lytims · Atnaujinta 2026-10-02 · NCT05861986

A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy

  • Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago
Renkami dalyviai2 fazė
Amžius nuo 5 iki 17 · Visoms lytims · Atnaujinta 2026-09-14 · NCT07287982

A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)

  • Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago
Renkami dalyviai1 fazė
Amžius 3 ir vyresni · Visoms lytims · Atnaujinta 2026-09-03 · NCT06555419

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

  • Lurie Childrens Hospital, Chicago
Renkami dalyviai
Amžius 3 ir vyresni · Visoms lytims · Atnaujinta 2026-08-19 · NCT05866419

A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety When Given Before Symptoms Appear in Babies With Genetically Diagnosed Spinal Muscular Atrophy (SMA)

  • Ann and Robert H Lurie Childrens Hospital of Chicago, Chicago
Renkami dalyviai3 fazė
0 Days – 42 Days · Visoms lytims · Atnaujinta 2026-08-18 · NCT07221669

ALS/MND Natural History Study Data Repository

  • Northwestern University, Chicago
Renkami dalyviaiStebimasis tyrimas
Amžius nuo 18 iki 90 · Visoms lytims · Atnaujinta 2026-05-20 · NCT05966038

Iš ClinicalTrials.gov, duomenys gauti 2026-10-05. Kiekvienas tyrimas nustato savo tinkamumo kriterijus; tyrimo komanda sprendžia, kas gali dalyvauti.