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A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Boston Children's Hospital, Boston
Renkami dalyviai2 fazė
Amžius nuo 5 iki 17 · Visoms lytims · Atnaujinta 2026-09-14 · NCT07287982A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)
- Boston Children's Hospital, Boston
Renkami dalyviai1 fazė
Amžius 3 ir vyresni · Visoms lytims · Atnaujinta 2026-09-03 · NCT06555419Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
- Boston Children's Hospital, Boston
Renkami dalyviai
Amžius 3 ir vyresni · Visoms lytims · Atnaujinta 2026-08-19 · NCT05866419ALS/MND Natural History Study Data Repository
- Lahey Clinic, Burlington
Renkami dalyviaiStebimasis tyrimas
Amžius nuo 18 iki 90 · Visoms lytims · Atnaujinta 2026-05-20 · NCT05966038Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders
- Boston Children's Hospital, Boston
Renkami dalyviaiStebimasis tyrimasLaukiami sveiki savanoriai
Amžius 5 ir vyresni · Visoms lytims · Atnaujinta 2026-04-09 · NCT06839469A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies
- Boston Children's Hospital, Boston
Renkami dalyviaiStebimasis tyrimas
Amžius nuo 18 iki 54 · Moterims · Atnaujinta 2026-03-09 · NCT05789758Iš ClinicalTrials.gov, duomenys gauti 2026-10-05. Kiekvienas tyrimas nustato savo tinkamumo kriterijus; tyrimo komanda sprendžia, kas gali dalyvauti.