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Kajian klinikal Gangguan Genetik di Florida
7 kajian untuk Gangguan Genetik sedang mencari peserta di lokasi di Florida.
Bandar di Florida
Teks kajian rasmi (Bahasa Inggeris)
Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network
- University of Miami Miller School of Medicine, Miami
Mengambil pesertaKajian pemerhatianSukarelawan sihat dialu-alukan
1 Month – 100 Years · Semua jantina · Dikemas kini 2 Okt 2026 · NCT02450851Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study
- University of Florida - Neurology, Gainesville
- USF Ataxia Research Center, Tampa
Mengambil pesertaKajian pemerhatianSukarelawan sihat dialu-alukan
Semua umur · Semua jantina · Dikemas kini 1 Sep 2026 · NCT06016946A Non-inferiority Pharmacokinetic and Safety/Tolerability Study of Two Different Doses of Weekly SC Alpha1-PI 15% Compared With Corresponding Standard IV Alpha1-PI in Participants With Alpha1-Antitrypsin Deficiency (AATD)
- GC2501 Study Site 103, Gainesville
- GC2501 Study Site 105, Miami
Mengambil pesertaFasa 3
Umur 18 hingga 80 · Semua jantina · Dikemas kini 11 Ogo 2026 · NCT07555483Safety of Anumigilimab (CSL324) in Adults With Sickle Cell Disease (SCD)
- The Foundation for Sickle Cell Disease, Hollywood
Mengambil pesertaFasa 2
Umur 18 ke atas · Semua jantina · Dikemas kini 5 Ogo 2026 · NCT07224360Rett Syndrome Registry
- Nicklaus Children's Hospital, Miami
Mengambil pesertaKajian pemerhatian
Umur 0 hingga 99 · Semua jantina · Dikemas kini 30 Jun 2026 · NCT05432349A Study Investigating the Effectiveness and Safety of Garadacimab for Treating Patients With Hereditary Angioedema (HAE)
- Sirven and Associates, Miami
Mengambil pesertaKajian pemerhatian
Umur 12 ke atas · Semua jantina · Dikemas kini 3 Jun 2026 · NCT07001280Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia
- Nicklaus Children's Hospital, Miami
- University of South Florida - 12901 Bruce B Downs, Tampa
Mengambil pesertaFasa 1/2
Semua umur · Semua jantina · Dikemas kini 22 Jan 2026 · NCT04159103Daripada ClinicalTrials.gov, data diperoleh pada 4 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.