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Kajian klinikal Gangguan Genetik di Ohio
7 kajian untuk Gangguan Genetik sedang mencari peserta di lokasi di Ohio.
Bandar di Ohio
Teks kajian rasmi (Bahasa Inggeris)
Study to Evaluate the Efficacy and Safety of BMN 333 Versus Vosoritide in Children With Achondroplasia
- Cincinnati Children's Hospital Medical Center, Cincinnati
Mengambil pesertaFasa 2/3
Umur 2 hingga 17 · Semua jantina · Dikemas kini 24 Sep 2026 · NCT07441876Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study
- Ohio State University - Neurology, Columbus
Mengambil pesertaKajian pemerhatianSukarelawan sihat dialu-alukan
Semua umur · Semua jantina · Dikemas kini 1 Sep 2026 · NCT06016946A Non-inferiority Pharmacokinetic and Safety/Tolerability Study of Two Different Doses of Weekly SC Alpha1-PI 15% Compared With Corresponding Standard IV Alpha1-PI in Participants With Alpha1-Antitrypsin Deficiency (AATD)
- GC2501 Study Site 104, Cleveland
Mengambil pesertaFasa 3
Umur 18 hingga 80 · Semua jantina · Dikemas kini 11 Ogo 2026 · NCT07555483Safety of Anumigilimab (CSL324) in Adults With Sickle Cell Disease (SCD)
- Ohio State University, Columbus
Mengambil pesertaFasa 2
Umur 18 ke atas · Semua jantina · Dikemas kini 5 Ogo 2026 · NCT07224360Prospective Clinical Assessment Study in Children With Hypochondroplasia
- Cincinnati Children's Hospital Medical Center, Cincinnati
Mengambil pesertaKajian pemerhatian
30 Months – 16 Years · Semua jantina · Dikemas kini 16 Jul 2026 · NCT06410976Rett Syndrome Registry
- Cincinnati Children's Hospital Medical Center, Cincinnati
- Nationwide Children's Hospital, Columbus
Mengambil pesertaKajian pemerhatian
Umur 0 hingga 99 · Semua jantina · Dikemas kini 30 Jun 2026 · NCT05432349Helix Research Network
- TriHealth (DNA Discovery), Cincinnati
- The Ohio State University (Genomic Health), Columbus
Mengambil pesertaKajian pemerhatianSukarelawan sihat dialu-alukan
Umur 18 ke atas · Semua jantina · Dikemas kini 23 Mac 2026 · NCT06057181Daripada ClinicalTrials.gov, data diperoleh pada 4 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.