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Kajian klinikal Gangguan Genetik di Philadelphia, PA
9 kajian untuk Gangguan Genetik sedang mencari peserta di lokasi dalam dan sekitar Philadelphia (dalam lingkungan kira-kira 30 batu). Buka kajian untuk melihat siapa yang layak menyertai dan cara menghubungi pasukan kajian.
Teks kajian rasmi (Bahasa Inggeris)
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Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network
Mengambil pesertaKajian pemerhatianSukarelawan sihat dialu-alukan
- University of Pennsylvania, Philadelphia
- Children's Hospital of Philadelphia, Philadelphia
Study to Evaluate the Efficacy and Safety of BMN 333 Versus Vosoritide in Children With Achondroplasia
Mengambil pesertaFasa 2/3
- Children's Hospital of Philadelphia, Philadelphia
- Nemours Children's Health, Wilmington · 25 mi jauh
Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study
Mengambil pesertaKajian pemerhatianSukarelawan sihat dialu-alukan
- Children's Hospital of Philadelphia, Philadelphia
Rett Syndrome Registry
Mengambil pesertaKajian pemerhatian
- Children's Hospital of Philadelphia, Philadelphia
Rifampin in CYP24A1-related Hypercalcemia and Hypercalciuria
Mengambil pesertaFasa 2
- Children's Hospital of Philadelphia, Philadelphia
ARPKD Database Study
Mengambil pesertaKajian pemerhatian
- Children's Hospital of Philadelphia, Philadelphia
A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study
Mengambil pesertaFasa 1/2
- The Children's Hospital of Philadelphia (CHOP), Philadelphia
Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia
Mengambil pesertaFasa 1/2
- Children's Hospital of Philadelphia (CHOP), Philadelphia
STXBP1 and SYNGAP1 Related Disorders Natural History Study
Mengambil pesertaKajian pemerhatian
- The Children's Hospital of Philadelphia, Philadelphia
Kajian Gangguan Genetik di bandar lain
- Washington, DC12 kajian
- Houston, TX8 kajian
- Durham, NC7 kajian
- Boston, MA6 kajian
- Los Angeles, CA6 kajian
- Mountain View, CA6 kajian
- Miami, FL5 kajian
- New York City, NY5 kajian
- San Diego, CA5 kajian
- Columbus, OH4 kajian
- Cincinnati, OH4 kajian
- Aurora, CO4 kajian
Kajian lain di Philadelphia
- Kanser (semua jenis)59 kajian
- Kanser Payudara56 kajian
- Kanser Paru-paru Bukan Sel Kecil51 kajian
- Kanser Metastatik46 kajian
- Kanser Kolorektal44 kajian
- Kanser Ovari44 kajian
- Kanser Prostat44 kajian
- Kanser Paru-paru36 kajian
- Leukemia Mieloid Akut34 kajian
- Kegagalan Jantung31 kajian
- Kanser Endometrium28 kajian
- Depresi26 kajian
Daripada ClinicalTrials.gov, data diperoleh pada 5 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.