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Kajian klinikal Leukoensefalopati di Pennsylvania
4 kajian untuk Leukoensefalopati sedang mencari peserta di lokasi di Pennsylvania.
Bandar di Pennsylvania
Teks kajian rasmi (Bahasa Inggeris)
An Open-Label Exploratory Study of Fosigotifator in Participants With Vanishing White Matter Disease
- Children's Hospital of Philadelphia, Philadelphia
Mengambil pesertaFasa 1/2
6 Months · Semua jantina · Dikemas kini 24 Sep 2026 · NCT05757141Longitudinal Study of Neurodegenerative Disorders
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
Mengambil pesertaKajian pemerhatian
Semua umur · Semua jantina · Dikemas kini 9 Feb 2026 · NCT03333200North American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC)
- The Children's Hospital of Philadelphia, Philadelphia
- Children's Hospital of Pittsburgh, Pittsburgh
Mengambil pesertaKajian pemerhatianSukarelawan sihat dialu-alukan
Semua umur · Semua jantina · Dikemas kini 4 Feb 2026 · NCT01694940The Myelin Disorders Biorepository Project
- The Children's Hospital of Philadelphia, Philadelphia
- University of Pennsylvania, Philadelphia
- University of Pittsburgh Medical Center, Pittsburgh
Mengambil pesertaKajian pemerhatian
Semua umur · Semua jantina · Dikemas kini 23 Okt 2025 · NCT03047369Daripada ClinicalTrials.gov, data diperoleh pada 4 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.