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Kajian klinikal Penyakit Jarang di California

10 kajian untuk Penyakit Jarang sedang mencari peserta di lokasi di California.

Bandar di California

Teks kajian rasmi (Bahasa Inggeris)

Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network

  • University of California, Los Angeles, Los Angeles
  • University of California, Irvine Medical Center, Orange
  • Stanford University, Stanford
  • dan 2 lagi
Mengambil pesertaKajian pemerhatianSukarelawan sihat dialu-alukan
1 Month – 100 Years · Semua jantina · Dikemas kini 2 Okt 2026 · NCT02450851

A Study of SGT-212 Gene Therapy in Friedreich's Ataxia

  • The University of California, Los Angeles (UCLA), Los Angeles
Mengambil pesertaFasa 1
Umur 18 hingga 40 · Semua jantina · Dikemas kini 29 Sep 2026 · NCT07180355

A First-in-human Study of KK8123 in Adults With X-linked Hypophosphatemia

  • University of California - San Francisco, San Francisco
Mengambil pesertaFasa 1/2
Umur 18 hingga 65 · Semua jantina · Dikemas kini 21 Sep 2026 · NCT06525636

Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study

  • UCLA Ataxia Center, Los Angeles
Mengambil pesertaKajian pemerhatianSukarelawan sihat dialu-alukan
Semua umur · Semua jantina · Dikemas kini 1 Sep 2026 · NCT06016946

International Rare Brain Tumor Registry

  • Children's Hospital Los Angeles, Los Angeles
  • University of California San Francisco, San Francisco
Mengambil pesertaKajian pemerhatian
Sehingga umur 45 · Semua jantina · Dikemas kini 7 Ogo 2026 · NCT05697874

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

  • University of California - Irvine Medical Center, Irvine
Mengambil pesertaFasa 2
Umur 18 ke atas · Semua jantina · Dikemas kini 23 Jun 2026 · NCT07123155

A Study of AAV9 Gene Therapy in Participants With Canavan Disease (CANaspire Clinical Trial)

  • UCSF Benioff Children's Hospital Oakland, Oakland
Mengambil pesertaFasa 1/2
30 Months · Semua jantina · Dikemas kini 17 Apr 2026 · NCT04998396

The ExTINGUISH Trial of Inebilizumab in NMDAR Encephalitis

  • Children's Hospital of Orange County, Orange
  • UC Irvine, Orange
  • UC Davis, Sacramento
Mengambil pesertaFasa 2
Umur 12 ke atas · Semua jantina · Dikemas kini 1 Jul 2025 · NCT04372615

Prospective Observational International Registry of Patients With Newly Diagnosed Peripheral T Cell Lymphoma.

  • Stanford University, Stanford
Mengambil pesertaKajian pemerhatian
Umur 18 ke atas · Semua jantina · Dikemas kini 6 Mei 2025 · NCT03964480

Epilepsy Learning Healthcare System (ELHS)

  • Children's Hospital Los Angeles, Los Angeles
  • University of Southern California, Los Angeles
Mengambil pesertaKajian pemerhatian
Semua umur · Semua jantina · Dikemas kini 30 Ogo 2024 · NCT06265103

Daripada ClinicalTrials.gov, data diperoleh pada 5 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.