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Kajian klinikal Penyakit Jarang di Pennsylvania
7 kajian untuk Penyakit Jarang sedang mencari peserta di lokasi di Pennsylvania.
Bandar di Pennsylvania
Teks kajian rasmi (Bahasa Inggeris)
Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network
- University of Pennsylvania, Philadelphia
- Children's Hospital of Philadelphia, Philadelphia
Mengambil pesertaKajian pemerhatianSukarelawan sihat dialu-alukan
1 Month – 100 Years · Semua jantina · Dikemas kini 2 Okt 2026 · NCT02450851A Study of SGT-212 Gene Therapy in Friedreich's Ataxia
- The Children's Hospital of Philadelphia (CHOP), Philadelphia
Mengambil pesertaFasa 1
Umur 18 hingga 40 · Semua jantina · Dikemas kini 29 Sep 2026 · NCT07180355Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study
- Children's Hospital of Philadelphia, Philadelphia
Mengambil pesertaKajian pemerhatianSukarelawan sihat dialu-alukan
Semua umur · Semua jantina · Dikemas kini 1 Sep 2026 · NCT06016946Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)
- University of Pennsylvania, Philadelphia
- University of Pittsburgh School of Medicine, Pittsburgh
Mengambil pesertaFasa 2
Umur 18 ke atas · Semua jantina · Dikemas kini 23 Jun 2026 · NCT07123155A Randomized Study of SPK-10001 Gene Therapy in Participants With Huntington's Disease
- University of Pennsylvania, Philadelphia
- University of Pittsburg, Pittsburgh
Mengambil pesertaFasa 1/2
Umur 25 hingga 65 · Semua jantina · Dikemas kini 5 Mei 2026 · NCT06826612The ExTINGUISH Trial of Inebilizumab in NMDAR Encephalitis
- University of Pennsylvania, Philadelphia
- University of Pittsburgh, Pittsburgh
Mengambil pesertaFasa 2
Umur 12 ke atas · Semua jantina · Dikemas kini 1 Jul 2025 · NCT04372615Epilepsy Learning Healthcare System (ELHS)
- Penn State Hershey, Hershey
- Children's Hospital of Philadelphia (CHOP), Philadelphia
Mengambil pesertaKajian pemerhatian
Semua umur · Semua jantina · Dikemas kini 30 Ogo 2024 · NCT06265103Daripada ClinicalTrials.gov, data diperoleh pada 5 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.