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Kajian klinikal Penyakit Sel Sabit di Massachusetts
10 kajian untuk Penyakit Sel Sabit sedang mencari peserta di lokasi di Massachusetts.
Bandar di Massachusetts
Teks kajian rasmi (Bahasa Inggeris)
A Study to Evaluate How Well Etavopivat Works in People With Sickle Cell Disease
- Boston Children's Hospital, Boston
- Boston Medical Center, Boston
Mengambil pesertaFasa 3
Umur 12 ke atas · Semua jantina · Dikemas kini 17 Sep 2026 · NCT06612268A Phase I/II Study of ITU512 in Healthy Participants and Patients With Sickle Cell Disease
- Boston Childrens Hospital, Boston
Mengambil pesertaFasa 1/2Sukarelawan sihat dialu-alukan
Umur 12 hingga 55 · Semua jantina · Dikemas kini 9 Sep 2026 · NCT06546670A Study to Evaluate BMS-986470 in Healthy Volunteers and Participants With Sickle Cell Disease
- Local Institution - 0024, Boston
- Boston Medical Center, Boston
Mengambil pesertaFasa 1/2Sukarelawan sihat dialu-alukan
Umur 18 ke atas · Semua jantina · Dikemas kini 18 Ogo 2026 · NCT06481306ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders
- Massachusetts General Hospital Comprehensive Hemophilia and Thrombosis Treatment Center, Boston
Mengambil pesertaKajian pemerhatian
Semua umur · Semua jantina · Dikemas kini 17 Ogo 2026 · NCT04398628Comparing the Effectiveness of Matched Related Donor Hematopoietic Stem Cell Transplantation to Disease Modifying Therapy in Pediatric Patients With Sickle Cell Disease
- Boston Children's Hospital (MRD-HCT), Boston
- Boston Children's Hospital (NT-DMT), Boston
Mengambil pesertaKajian pemerhatian
Umur 3 hingga 20 · Semua jantina · Dikemas kini 4 Jun 2026 · NCT06941389Promoting Resilience Among Adolescents and Young Adults With Sickle Cell Disease
- Boston Children's Hospital, Boston
Mengambil peserta
Umur 8 hingga 25 · Semua jantina · Dikemas kini 5 Mei 2026 · NCT06555939Hematopoietic Stem Cell BCL11A Enhancer Gene Editing for Severe β-Hemoglobinopathies
- Boston Children's Hospital, Boston
Mengambil pesertaFasa 1
Umur 13 hingga 40 · Semua jantina · Dikemas kini 3 Feb 2026 · NCT06647979A Long-term Follow-up Study in Patients Who Received BEAM-101
- Boston Children's Hospital, Boston
Mengambil pesertaKajian pemerhatian
Umur 14 hingga 37 · Semua jantina · Dikemas kini 28 Jan 2026 · NCT07373639A Pilot Study on Neuroimaging in SCD: Part of The Boston Consortium to Cure Sickle Cell Disease
- Boston Children's Hospital, Boston
Mengambil pesertaKajian pemerhatian
Umur 8 hingga 18 · Semua jantina · Dikemas kini 12 Dis 2025 · NCT04166526Study of the Role of Genetic Modifiers in Hemoglobinopathies
- Boston Children's Hospital, Boston
Mengambil pesertaKajian pemerhatian
Umur 2 ke atas · Semua jantina · Dikemas kini 20 Mac 2024 · NCT05799118Daripada ClinicalTrials.gov, data diperoleh pada 5 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.