Utama › Atrofi Otot Spinal › Arkansas
Kajian klinikal Atrofi Otot Spinal di Arkansas
4 kajian untuk Atrofi Otot Spinal sedang mencari peserta di lokasi di Arkansas.
Bandar di Arkansas
Teks kajian rasmi (Bahasa Inggeris)
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
- University of Arkansas for Medical Sciences, Little Rock
Mengambil pesertaFasa 4
3 Months – 24 Months · Semua jantina · Dikemas kini 2 Okt 2026 · NCT05861986A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Arkansas Children's Hospital, Little Rock
Mengambil pesertaFasa 2
Umur 5 hingga 17 · Semua jantina · Dikemas kini 14 Sep 2026 · NCT07287982A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
- University of Arkansas for Medical Sciences, Little Rock
Mengambil pesertaFasa 4
3 Months – 24 Months · Semua jantina · Dikemas kini 10 Sep 2026 · NCT05861999Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
- Arkansas Children's Hospital, Little Rock
Mengambil pesertaKajian pemerhatian
Semua umur · Semua jantina · Dikemas kini 31 Jan 2025 · NCT04174157Daripada ClinicalTrials.gov, data diperoleh pada 5 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.