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Kajian klinikal Atrofi Otot Spinal sedang mengambil peserta di AS
23 kajian untuk Atrofi Otot Spinal sedang mengambil peserta di lokasi seluruh Amerika Syarikat.
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- New York City, NY9 kajian
- Mountain View, CA9 kajian
- Philadelphia, PA7 kajian
- Chicago, IL6 kajian
- Norfolk, VA6 kajian
- Grand Rapids, MI6 kajian
- Boston, MA5 kajian
- Houston, TX5 kajian
- Lewisville, TX4 kajian
- Little Rock, AR4 kajian
- Phoenix, AZ4 kajian
- Aurora, CO4 kajian
- Memphis, TN3 kajian
- Durham, NC3 kajian
- Cedar Rapids, IA3 kajian
- Columbia, MO3 kajian
- Orlando, FL3 kajian
- Fort Worth, TX3 kajian
- Portland, OR3 kajian
- Minneapolis, MN3 kajian
- Charlottesville, VA3 kajian
- Harrisburg, PA3 kajian
- Atlanta, GA3 kajian
- Dallas, TX3 kajian
- Gainesville, FL3 kajian
- Orange, CA3 kajian
Mengikut negeri
- Arizona4 kajian
- Arkansas4 kajian
- California11 kajian
- Colorado4 kajian
- Florida8 kajian
- Georgia3 kajian
- Illinois6 kajian
- Iowa3 kajian
- Massachusetts6 kajian
- Michigan6 kajian
- Minnesota3 kajian
- Missouri4 kajian
- New York10 kajian
- North Carolina3 kajian
- Oregon3 kajian
- Pennsylvania8 kajian
- Tennessee3 kajian
- Texas10 kajian
- Virginia7 kajian
Kajian yang dikemas kini baru-baru ini
Teks kajian rasmi (Bahasa Inggeris)
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
Mengambil pesertaFasa 4
3 Months – 24 Months · Semua jantina · Dikemas kini 2 Okt 2026 · NCT05861986A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy
Mengambil pesertaFasa 2
Sehingga umur 2 · Semua jantina · Dikemas kini 2 Okt 2026 · NCT07047144A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety in Participants Aged 15 to 60 Years With Spinal Muscular Atrophy (SMA) Who Are Either New to SMA Treatment or Were Previously Treated With Risdiplam
Mengambil pesertaFasa 3
Umur 15 hingga 60 · Semua jantina · Dikemas kini 2 Okt 2026 · NCT07444476A Registry of Cases of Spinal Muscular Atrophy
Mengambil pesertaKajian pemerhatian
Semua umur · Semua jantina · Dikemas kini 30 Sep 2026 · NCT07805278ASsessing The REAl-world Safety & Effectiveness of Spinal Muscular Atrophy Participants Treated With Intrathecal Onasemnogene Abeparvovec-brve (OAV101B) (ITVISMA®): A U.S. Pragmatic Multicenter Study (STREAM)
Mengambil pesertaFasa 4
Umur 2 hingga 100 · Semua jantina · Dikemas kini 18 Sep 2026 · NCT07448610A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
Mengambil pesertaFasa 2
Umur 5 hingga 17 · Semua jantina · Dikemas kini 14 Sep 2026 · NCT07287982A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
Mengambil pesertaFasa 4
3 Months – 24 Months · Semua jantina · Dikemas kini 10 Sep 2026 · NCT05861999A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)
Mengambil pesertaFasa 1
Umur 3 ke atas · Semua jantina · Dikemas kini 3 Sep 2026 · NCT06555419Interfacing With NeuroTechnology to Expand Neural Throughput (INTENT)
Mengambil peserta
Umur 18 hingga 80 · Semua jantina · Dikemas kini 2 Sep 2026 · NCT07521930Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
Mengambil peserta
Umur 3 ke atas · Semua jantina · Dikemas kini 19 Ogo 2026 · NCT05866419A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety When Given Before Symptoms Appear in Babies With Genetically Diagnosed Spinal Muscular Atrophy (SMA)
Mengambil pesertaFasa 3
0 Days – 42 Days · Semua jantina · Dikemas kini 18 Ogo 2026 · NCT07221669A Study to Learn About the Safety and Effects of Salanersen (BIIB115) When Given to Babies With Spinal Muscular Atrophy (SMA) Who Were Previously Treated With Onasemnogene Abeparvovec
Mengambil pesertaFasa 3
0 Days – 7 Months · Semua jantina · Dikemas kini 11 Ogo 2026 · NCT07444450Exploring the Physiologic, Pharmacodynamic, and Clinical Responses of Skeletal Muscle in Patients With Spinal Muscular Atrophy Treated With SMN-Directed Therapies
Mengambil pesertaKajian pemerhatian
Umur 5 hingga 20 · Semua jantina · Dikemas kini 9 Jul 2026 · NCT06532474Clinical Procedures to Support Research in ALS
Mengambil pesertaKajian pemerhatian
Umur 18 ke atas · Semua jantina · Dikemas kini 15 Jun 2026 · NCT03489278ALS/MND Natural History Study Data Repository
Mengambil pesertaKajian pemerhatian
Umur 18 hingga 90 · Semua jantina · Dikemas kini 20 Mei 2026 · NCT05966038Characterizing Perceived Physical Fatigability in Nusinersen-treated SMA
Mengambil pesertaKajian pemerhatian
Umur 12 ke atas · Semua jantina · Dikemas kini 14 Mei 2026 · NCT06955897Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders
Mengambil pesertaKajian pemerhatianSukarelawan sihat dialu-alukan
Umur 5 ke atas · Semua jantina · Dikemas kini 9 Apr 2026 · NCT06839469HABIT-ILE + FST in Children With SMA: Preliminary Effectiveness
Mengambil peserta
Umur 5 hingga 17 · Semua jantina · Dikemas kini 23 Mac 2026 · NCT07488338Gait and Bone Health in SMA
Mengambil pesertaKajian pemerhatian
Umur 8 hingga 50 · Semua jantina · Dikemas kini 18 Mac 2026 · NCT07400198Effects of Whole-body Electrical Muscle Stimulation Exercise on Adults With Neuromuscular Disease
Mengambil peserta
Umur 18 ke atas · Semua jantina · Dikemas kini 17 Mac 2026 · NCT07478172A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies
Mengambil pesertaKajian pemerhatian
Umur 18 hingga 54 · Wanita · Dikemas kini 9 Mac 2026 · NCT05789758Diagnostic Journey, Patient Experience, and Disparities in the Treatment of Spinal Muscular Atrophy (SMA) in the MedStar Health System
Mengambil pesertaKajian pemerhatian
Umur 18 ke atas · Semua jantina · Dikemas kini 16 Jan 2026 · NCT07223489Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
Mengambil pesertaKajian pemerhatian
Semua umur · Semua jantina · Dikemas kini 31 Jan 2025 · NCT04174157Daripada ClinicalTrials.gov, data diperoleh pada 4 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.