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Utama › Atrofi Otot Spinal › Colorado

Kajian klinikal Atrofi Otot Spinal di Colorado

4 kajian untuk Atrofi Otot Spinal sedang mencari peserta di lokasi di Colorado.

Bandar di Colorado

Teks kajian rasmi (Bahasa Inggeris)

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy

  • Children's Hospital of Colorado, Aurora
Mengambil pesertaFasa 4
3 Months – 24 Months · Semua jantina · Dikemas kini 2 Okt 2026 · NCT05861986

A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy

  • Children's Hospital Colorado, Aurora
Mengambil pesertaFasa 2
Sehingga umur 2 · Semua jantina · Dikemas kini 2 Okt 2026 · NCT07047144

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy

  • Children's Hospital of Colorado, Aurora
Mengambil pesertaFasa 4
3 Months – 24 Months · Semua jantina · Dikemas kini 10 Sep 2026 · NCT05861999

Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

  • Children's Hospital Colorado, Aurora
Mengambil pesertaKajian pemerhatian
Semua umur · Semua jantina · Dikemas kini 31 Jan 2025 · NCT04174157

Daripada ClinicalTrials.gov, data diperoleh pada 5 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.