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Kajian klinikal Atrofi Otot Spinal di Massachusetts
6 kajian untuk Atrofi Otot Spinal sedang mencari peserta di lokasi di Massachusetts.
Bandar di Massachusetts
Teks kajian rasmi (Bahasa Inggeris)
A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Boston Children's Hospital, Boston
Mengambil pesertaFasa 2
Umur 5 hingga 17 · Semua jantina · Dikemas kini 14 Sep 2026 · NCT07287982A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)
- Boston Children's Hospital, Boston
Mengambil pesertaFasa 1
Umur 3 ke atas · Semua jantina · Dikemas kini 3 Sep 2026 · NCT06555419Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
- Boston Children's Hospital, Boston
Mengambil peserta
Umur 3 ke atas · Semua jantina · Dikemas kini 19 Ogo 2026 · NCT05866419ALS/MND Natural History Study Data Repository
- Lahey Clinic, Burlington
Mengambil pesertaKajian pemerhatian
Umur 18 hingga 90 · Semua jantina · Dikemas kini 20 Mei 2026 · NCT05966038Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders
- Boston Children's Hospital, Boston
Mengambil pesertaKajian pemerhatianSukarelawan sihat dialu-alukan
Umur 5 ke atas · Semua jantina · Dikemas kini 9 Apr 2026 · NCT06839469A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies
- Boston Children's Hospital, Boston
Mengambil pesertaKajian pemerhatian
Umur 18 hingga 54 · Wanita · Dikemas kini 9 Mac 2026 · NCT05789758Daripada ClinicalTrials.gov, data diperoleh pada 5 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.