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Kajian klinikal Atrofi Otot Spinal di Massachusetts

6 kajian untuk Atrofi Otot Spinal sedang mencari peserta di lokasi di Massachusetts.

Bandar di Massachusetts

Teks kajian rasmi (Bahasa Inggeris)

A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)

  • Boston Children's Hospital, Boston
Mengambil pesertaFasa 1
Umur 3 ke atas · Semua jantina · Dikemas kini 3 Sep 2026 · NCT06555419

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

  • Boston Children's Hospital, Boston
Mengambil peserta
Umur 3 ke atas · Semua jantina · Dikemas kini 19 Ogo 2026 · NCT05866419

ALS/MND Natural History Study Data Repository

  • Lahey Clinic, Burlington
Mengambil pesertaKajian pemerhatian
Umur 18 hingga 90 · Semua jantina · Dikemas kini 20 Mei 2026 · NCT05966038

Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders

  • Boston Children's Hospital, Boston
Mengambil pesertaKajian pemerhatianSukarelawan sihat dialu-alukan
Umur 5 ke atas · Semua jantina · Dikemas kini 9 Apr 2026 · NCT06839469

A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies

  • Boston Children's Hospital, Boston
Mengambil pesertaKajian pemerhatian
Umur 18 hingga 54 · Wanita · Dikemas kini 9 Mac 2026 · NCT05789758

Daripada ClinicalTrials.gov, data diperoleh pada 5 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.