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Kliniske studier for Spinal muskelatrofi i California

11 studier for Spinal muskelatrofi søker deltakere på steder i California.

Byer i California

Offisiell studietekst (engelsk)

A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy

  • Children's Hospital of Orange County (CHOC), Orange
  • Stanford Neuroscience Health Center (SNHC), Palo Alto
RekruttererFase 2
Opp til 2 år · Alle kjønn · Oppdatert 2. okt. 2026 · NCT07047144

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy

  • Valley Children's Hospital, Madera
  • Stanford Univ Medical Center, Palo Alto
RekruttererFase 4
3 Months – 24 Months · Alle kjønn · Oppdatert 10. sep. 2026 · NCT05861999

A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)

  • Children's Hospital of Orange County, Orange
  • Stanford University Medical Center | Department of Neurology_Palo Alto, Palo Alto
RekruttererFase 1
Alder 3 og eldre · Alle kjønn · Oppdatert 3. sep. 2026 · NCT06555419

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

  • Children's Hospital Orange County, Orange
  • Stanford Medical Center, Palo Alto
  • Rady Children's Hospital, San Diego
Rekrutterer
Alder 3 og eldre · Alle kjønn · Oppdatert 19. aug. 2026 · NCT05866419

Clinical Procedures to Support Research in ALS

  • University of California, Irvine, Irvine
  • Stanford University, Palo Alto
  • California Pacific Medical Center, San Francisco
RekruttererObservasjonsstudie
Alder 18 og eldre · Alle kjønn · Oppdatert 15. jun. 2026 · NCT03489278

ALS/MND Natural History Study Data Repository

  • Loma Linda University Health, Loma Linda
  • Kaiser Permanente, Los Angeles
RekruttererObservasjonsstudie
Alder 18 til 90 · Alle kjønn · Oppdatert 20. mai 2026 · NCT05966038

Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders

  • Stanford University, Palo Alto
RekruttererObservasjonsstudieFrivillige helsepersonell ønskes velkommen
Alder 5 og eldre · Alle kjønn · Oppdatert 9. apr. 2026 · NCT06839469

A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies

  • Stanford Neuroscience Health Center, Palo Alto
RekruttererObservasjonsstudie
Alder 18 til 54 · Kvinner · Oppdatert 9. mar. 2026 · NCT05789758

Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

  • Children's Hospital of Los Angeles, Los Angeles
  • University of California Los Angeles Health, Los Angeles
  • Valley Children's Healthcare, Madera
  • og 3 flere
RekruttererObservasjonsstudie
Alle aldre · Alle kjønn · Oppdatert 31. jan. 2025 · NCT04174157

Fra ClinicalTrials.gov, data hentet 5. okt. 2026. Hver studie setter sine egne kvalifikasjonskrav; studieteamet avgjør hvem som kan delta.