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Kliniske studier for Spinal muskelatrofi i Florida
8 studier for Spinal muskelatrofi søker deltakere på steder i Florida.
Byer i Florida
Offisiell studietekst (engelsk)
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
- University of Florida Pediatrics, Gainesville
RekruttererFase 4
3 Months – 24 Months · Alle kjønn · Oppdatert 2. okt. 2026 · NCT05861986A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Rare Disease Research FL LLC, Kissimmee
RekruttererFase 2
Alder 5 til 17 · Alle kjønn · Oppdatert 14. sep. 2026 · NCT07287982A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
- University of Florida Pediatrics, Gainesville
RekruttererFase 4
3 Months – 24 Months · Alle kjønn · Oppdatert 10. sep. 2026 · NCT05861999A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)
- Nemours Children's Hospital, Orlando, Orlando
RekruttererFase 1
Alder 3 og eldre · Alle kjønn · Oppdatert 3. sep. 2026 · NCT06555419Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
- Nemours Children's Hospital, Florida, Orlando
Rekrutterer
Alder 3 og eldre · Alle kjønn · Oppdatert 19. aug. 2026 · NCT05866419Clinical Procedures to Support Research in ALS
- University of Miami, Miami
RekruttererObservasjonsstudie
Alder 18 og eldre · Alle kjønn · Oppdatert 15. jun. 2026 · NCT03489278ALS/MND Natural History Study Data Repository
- University of Florida, Gainesville
RekruttererObservasjonsstudie
Alder 18 til 90 · Alle kjønn · Oppdatert 20. mai 2026 · NCT05966038Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
- Golisano Children's Hospital of Southwest Florida, Fort Myers
- Jackson South Medical Center, Palmetto Bay
RekruttererObservasjonsstudie
Alle aldre · Alle kjønn · Oppdatert 31. jan. 2025 · NCT04174157Fra ClinicalTrials.gov, data hentet 5. okt. 2026. Hver studie setter sine egne kvalifikasjonskrav; studieteamet avgjør hvem som kan delta.