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Gara Jalqabaatti › Duchenne Muscular Dystrophy › Arkansas

Qorannoo klinikaalii Duchenne Muscular Dystrophy Arkansas keessatti

Qorannoo 7 Duchenne Muscular Dystrophy f Arkansas keessatti hirmaatuu jiru.

Magaalota Arkansas keessatti

Takkalaa qorannoo (Ingiliffa)

A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)

  • Arkansas Children's Hospital, Little Rock
Namoota walitti qabaa jiraSadarkaa 3
Umuriin 7 hanga 11 · Dhiroota · Haaromfame 28-Ful-2026 · NCT07160634

A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory Cohort

  • Arkansas Children's Hospital, Little Rock
Namoota walitti qabaa jiraSadarkaa 1
Umuriin 2 fi ol · Dhiroota · Haaromfame 11-Ful-2026 · NCT04626674

A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)

  • Arkansas Children's Hospital, Little Rock
Namoota walitti qabaa jiraSadarkaa 1/2
Umuriin 0 hanga 17 · Dhiroota · Haaromfame 08-Ado-2026 · NCT06138639

A Study Evaluating the Real-World Experience of Givinostat in Patients With Duchenne Muscular Dystrophy

  • Arkansas Children's Research Institute, Little Rock
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 6 fi ol · Saalaa hunda · Haaromfame 02-Ado-2026 · NCT07127978

PBGENE-DMD Phase 1/2a Safety and Preliminary Efficacy Study in Duchenne Muscular Dystrophy (FUNCTION-DMD)

  • Arkansas Children's Hospital, Little Rock
Namoota walitti qabaa jiraSadarkaa 1/2
Umuriin 2 hanga 7 · Dhiroota · Haaromfame 23-Wax-2026 · NCT07429240

Duchenne Electronic Health Record Study

  • Arkansas Children's Hospital, Little Rock
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 27-Cam-2026 · NCT07609394

Open-label Study of WVE-N531 in Patients With Duchenne Muscular Dystrophy (FORWARD-53)

  • Arkansas Children's Hospital, Little Rock
Namoota walitti qabaa jiraSadarkaa 1/2
Umuriin 4 hanga 18 · Dhiroota · Haaromfame 15-Mud-2025 · NCT04906460

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.