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Gara Jalqabaatti › Duchenne Muscular Dystrophy

Qorannoo klinikaalii Duchenne Muscular Dystrophy Ameerikaa Keessatti hirmaatuu

Qorannoo 26 Duchenne Muscular Dystrophy f bakka adda addaa Ameerikaa Keessatti hirmaatuu jiru.

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A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)

Namoota walitti qabaa jiraSadarkaa 3
Umuriin 7 hanga 11 · Dhiroota · Haaromfame 28-Ful-2026 · NCT07160634

Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMIT

Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 2 fi ol · Dhiroota · Haaromfame 24-Ful-2026 · NCT06564974

Sodium/Glucose Cotransporter-2 Inhibitors (SGLT2i) Therapy in Duchenne Cardiomyopathy

Namoota walitti qabaa jiraSadarkaa 1
Umuriin 8 hanga 18 · Dhiroota · Haaromfame 24-Hag-2026 · NCT07172971

The Baby Duchenne Study: Characterizing Developmental and Clinical Outcomes in the First Three Years in Children With Duchenne Muscular Dystrophy

Namoota walitti qabaa jiraQorannoo ilaalaa
0 Days – 3 Years · Dhiroota · Haaromfame 19-Hag-2026 · NCT07092540

Evaluating VM100 Nutritional Supplement for Improving Quality of Life in Duchenne Muscular Dystrophy Patients

Namoota walitti qabaa jira
Umuriin 6 fi ol · Dhiroota · Haaromfame 17-Hag-2026 · NCT07766980

Once Weekly Infant Corticosteroid Trial for DMD

Namoota walitti qabaa jiraSadarkaa 4
1 Month – 30 Months · Dhiroota · Haaromfame 14-Hag-2026 · NCT05412394

Modeling Mortality in Duchenne Muscular Dystrophy Cardiomyopathy: Identification of Surrogate Outcome Measures for DMD Drug Trials

Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 28-Ado-2026 · NCT07674758

A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)

Namoota walitti qabaa jiraSadarkaa 1/2
Umuriin 0 hanga 17 · Dhiroota · Haaromfame 08-Ado-2026 · NCT06138639

A Study Evaluating the Real-World Experience of Givinostat in Patients With Duchenne Muscular Dystrophy

Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 6 fi ol · Saalaa hunda · Haaromfame 02-Ado-2026 · NCT07127978

PBGENE-DMD Phase 1/2a Safety and Preliminary Efficacy Study in Duchenne Muscular Dystrophy (FUNCTION-DMD)

Namoota walitti qabaa jiraSadarkaa 1/2
Umuriin 2 hanga 7 · Dhiroota · Haaromfame 23-Wax-2026 · NCT07429240

Duchenne Electronic Health Record Study

Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 27-Cam-2026 · NCT07609394

Wearable Technology to Evaluate Hyperglycemia and HRV in DMD

Namoota walitti qabaa jiraQorannoo ilaalaaHojjettoota fayyaa simatamoo
Umuriin 10 fi ol · Dhiroota · Haaromfame 22-Cam-2026 · NCT06124196

Vasodilator and Exercise Study for DMD (VASO-REx)

Namoota walitti qabaa jiraSadarkaa 2
Umuriin 6 fi ol · Dhiroota · Haaromfame 15-Cam-2026 · NCT06290713

The Duchenne Registry

Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 08-Cam-2026 · NCT02069756

Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders

Namoota walitti qabaa jiraQorannoo ilaalaaHojjettoota fayyaa simatamoo
Umuriin 5 fi ol · Saalaa hunda · Haaromfame 09-Elb-2026 · NCT06839469

Urinary Titin Biomarker in DMD

Namoota walitti qabaa jiraHojjettoota fayyaa simatamoo
Umuriin 2 hanga 10 · Dhiroota · Haaromfame 08-Elb-2026 · NCT07332013

Trial of Cell Based Therapy for DMD

Namoota walitti qabaa jiraSadarkaa 1
Umuriin 18 fi ol · Saalaa hunda · Haaromfame 04-Bit-2026 · NCT06692426

Open-label Study of WVE-N531 in Patients With Duchenne Muscular Dystrophy (FORWARD-53)

Namoota walitti qabaa jiraSadarkaa 1/2
Umuriin 4 hanga 18 · Dhiroota · Haaromfame 15-Mud-2025 · NCT04906460

Extracellular RNA Biomarkers of Duchenne Muscular Dystrophy

Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 5 fi ol · Saalaa hunda · Haaromfame 24-Sad-2025 · NCT05016908

Biomarker Development for Muscular Dystrophies

Namoota walitti qabaa jiraQorannoo ilaalaaHojjettoota fayyaa simatamoo
Umuriin 5 fi ol · Saalaa hunda · Haaromfame 24-Sad-2025 · NCT05019625

Wearable Technology to Evaluate Hyperglycemia and HRV in DMD - Longitudinal Aim

Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 10 fi ol · Dhiroota · Haaromfame 06-Sad-2025 · NCT06093100

Magnetic Resonance Imaging and Biomarkers for Muscular Dystrophy

Namoota walitti qabaa jiraQorannoo ilaalaaHojjettoota fayyaa simatamoo
Umuriin 5 hanga 62 · Dhiroota · Haaromfame 15-Onk-2025 · NCT01484678

DMD Voice: Qualitative Interviews With Patients and Caregivers

Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 10 fi ol · Dhiroota · Haaromfame 30-Elb-2025 · NCT06925269

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