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Gara Jalqabaatti › Duchenne Muscular Dystrophy › California

Qorannoo klinikaalii Duchenne Muscular Dystrophy California keessatti

Qorannoo 6 Duchenne Muscular Dystrophy f California keessatti hirmaatuu jiru.

Magaalota California keessatti

Takkalaa qorannoo (Ingiliffa)

Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMIT

  • Loma Linda University Pediatric Subspecialty Clinics, Loma Linda
  • Children's Hospital Los Angeles, Los Angeles
  • Valley Children's Hospital, Madera
  • fi 2 dabalataa
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 2 fi ol · Dhiroota · Haaromfame 24-Ful-2026 · NCT06564974

A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory Cohort

  • University of California, San Diego, La Jolla
  • University of California, Los Angeles, Los Angeles
  • Stanford University, Palo Alto
  • fi 1 dabalataa
Namoota walitti qabaa jiraSadarkaa 1
Umuriin 2 fi ol · Dhiroota · Haaromfame 11-Ful-2026 · NCT04626674

Modeling Mortality in Duchenne Muscular Dystrophy Cardiomyopathy: Identification of Surrogate Outcome Measures for DMD Drug Trials

  • UC Davis, Sacramento
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 28-Ado-2026 · NCT07674758

A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)

  • University of California, Los Angeles Medical Center, Los Angeles
  • University of California, Davis, Sacramento
  • University of California, San Diego
Namoota walitti qabaa jiraSadarkaa 1/2
Umuriin 0 hanga 17 · Dhiroota · Haaromfame 08-Ado-2026 · NCT06138639

Duchenne Electronic Health Record Study

  • UC Davis Health, Sacramento
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 27-Cam-2026 · NCT07609394

Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders

  • Stanford University, Palo Alto
Namoota walitti qabaa jiraQorannoo ilaalaaHojjettoota fayyaa simatamoo
Umuriin 5 fi ol · Saalaa hunda · Haaromfame 09-Elb-2026 · NCT06839469

Kanneen ClinicalTrials.gov irraa argaman, daataa 05-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.