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Qorannoo klinikaalii Ataxia Friedreich Pennsylvania keessatti
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A Study of SGT-212 Gene Therapy in Friedreich's Ataxia
- The Children's Hospital of Philadelphia (CHOP), Philadelphia
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Umuriin 18 hanga 40 · Saalaa hunda · Haaromfame 29-Ful-2026 · NCT07180355An Open-Label Study of CTI-1601 in Subjects With Friedreich's Ataxia
- Children's Hospital of the University of Pennsylvania (CHOP), Philadelphia
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Umuriin 2 hanga 60 · Saalaa hunda · Haaromfame 03-Ful-2026 · NCT06447025Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study
- Children's Hospital of Philadelphia, Philadelphia
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Umuriin hundi · Saalaa hunda · Haaromfame 01-Ful-2026 · NCT06016946A Study to Learn More About the Long-Term Safety of BIIB141 (Omaveloxolone) in Participants With Friedreich's Ataxia Who Are Prescribed it by Their Own Doctors
- Children's Hospital of Philadelphia, Philadelphia
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Umuriin 16 fi ol · Saalaa hunda · Haaromfame 28-Elb-2026 · NCT06623890Kanneen ClinicalTrials.gov irraa argaman, daataa 05-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.