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Qorannoo klinikaalii Ataxia Friedreich Pennsylvania keessatti

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A Study of SGT-212 Gene Therapy in Friedreich's Ataxia

  • The Children's Hospital of Philadelphia (CHOP), Philadelphia
Namoota walitti qabaa jiraSadarkaa 1
Umuriin 18 hanga 40 · Saalaa hunda · Haaromfame 29-Ful-2026 · NCT07180355

An Open-Label Study of CTI-1601 in Subjects With Friedreich's Ataxia

  • Children's Hospital of the University of Pennsylvania (CHOP), Philadelphia
Namoota walitti qabaa jiraSadarkaa 2
Umuriin 2 hanga 60 · Saalaa hunda · Haaromfame 03-Ful-2026 · NCT06447025

Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study

  • Children's Hospital of Philadelphia, Philadelphia
Namoota walitti qabaa jiraQorannoo ilaalaaHojjettoota fayyaa simatamoo
Umuriin hundi · Saalaa hunda · Haaromfame 01-Ful-2026 · NCT06016946

A Study to Learn More About the Long-Term Safety of BIIB141 (Omaveloxolone) in Participants With Friedreich's Ataxia Who Are Prescribed it by Their Own Doctors

  • Children's Hospital of Philadelphia, Philadelphia
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 16 fi ol · Saalaa hunda · Haaromfame 28-Elb-2026 · NCT06623890

Kanneen ClinicalTrials.gov irraa argaman, daataa 05-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.