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Takkalaa qorannoo (Ingiliffa)

A Gaucher Disease Gene Therapy Trial With FLT201

  • Kaiser Permanente - CA, Los Angeles
  • UCLA Health, Los Angeles
  • University of California, San Francisco (UCSF), San Francisco
Namoota walitti qabaa jiraSadarkaa 3
Umuriin 18 fi ol · Saalaa hunda · Haaromfame 03-Ful-2026 · NCT07223944

International Collaborative Gaucher Group (ICGG) Gaucher Disease Registry & Pregnancy Sub-registry

  • Tower Hematology Oncology Medical Group- Site Number : 840056, Beverly Hills
  • University of California at Irvine- Site Number : 840036, Irvine
  • Southern California Permanente Medical Group- Site Number : 840108, Los Angeles
  • fi 4 dabalataa
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 14-Elb-2026 · NCT00358943

Registry of Patients Diagnosed With Lysosomal Storage Diseases

  • University of California San Francisco, San Francisco
Namoota walitti qabaa jiraQorannoo ilaalaa
Hanga umuriin 64 · Saalaa hunda · Haaromfame 08-Elb-2026 · NCT05619900

PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)

  • University of California, San Francisco
Namoota walitti qabaa jiraSadarkaa 1
Umuriin 18 hanga 50 · Dubartoota · Haaromfame 17-Bit-2026 · NCT04532047

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.