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Gaucher Disease Outcome Survey (GOS)

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Umuriin hundi · Saalaa hunda · Haaromfame 15-Ful-2026 · NCT03291223

A Long-term Follow-up Study of Gaucher Disease

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Umuriin hundi · Saalaa hunda · Haaromfame 03-Ful-2026 · NCT03190837

A Gaucher Disease Gene Therapy Trial With FLT201

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Umuriin 18 fi ol · Saalaa hunda · Haaromfame 03-Ful-2026 · NCT07223944

Advancing Integrated Therapies for Gaucher Disease

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3 Months – 75 Years · Saalaa hunda · Haaromfame 11-Hag-2026 · NCT07758816

MAGNETIC RESONANCE SPECTROSCOPY BIOMARKERS IN TYPE 3 GAUCHER DISEASE (GD3)

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Umuriin 18 hanga 80 · Saalaa hunda · Haaromfame 04-Hag-2026 · NCT05586243

Oxidative Stress and Inflammatory Biomarkers in Gaucher Disease

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Umuriin 18 hanga 75 · Saalaa hunda · Haaromfame 13-Ado-2026 · NCT02437396

International Collaborative Gaucher Group (ICGG) Gaucher Disease Registry & Pregnancy Sub-registry

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Umuriin hundi · Saalaa hunda · Haaromfame 14-Elb-2026 · NCT00358943

Registry of Patients Diagnosed With Lysosomal Storage Diseases

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Hanga umuriin 64 · Saalaa hunda · Haaromfame 08-Elb-2026 · NCT05619900

Extracellular Vesicles as Potential Biomarkers and Therapeutic Target in Gaucher Disease

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Umuriin 18 hanga 80 · Saalaa hunda · Haaromfame 06-Elb-2026 · NCT05843552

Study of CAR T-Cells Targeting the GD2 With IL-15+iCaspase9 for Relapsed/Refractory Neuroblastoma or Relapsed/Refractory Osteosarcoma

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18 Months · Saalaa hunda · Haaromfame 27-Bit-2026 · NCT03721068

PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)

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Umuriin 18 hanga 50 · Dubartoota · Haaromfame 17-Bit-2026 · NCT04532047

Longitudinal Study of Neurodegenerative Disorders

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Umuriin hundi · Saalaa hunda · Haaromfame 09-Gur-2026 · NCT03333200

Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

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2 Months – 60 Years · Saalaa hunda · Haaromfame 13-Ama-2026 · NCT04528355

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

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2 Months – 55 Years · Saalaa hunda · Haaromfame 15-Mud-2025 · NCT01962415

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.