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Gara Jalqabaatti › Dhibbee Gaucher › Pennsylvania

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Takkalaa qorannoo (Ingiliffa)

A Gaucher Disease Gene Therapy Trial With FLT201

  • Children's Hospital of Philadelphia, Philadelphia
  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Namoota walitti qabaa jiraSadarkaa 3
Umuriin 18 fi ol · Saalaa hunda · Haaromfame 03-Ful-2026 · NCT07223944

International Collaborative Gaucher Group (ICGG) Gaucher Disease Registry & Pregnancy Sub-registry

  • Penn State Health Milton South Hershey Medical Center- Site Number : 840126, Hershey
  • Children's Hospital of Philadelphia HUP Medical Genetics- Site Number : 840089, Philadelphia
  • Children's Hospital of Philadelphia- Site Number : 840034, Philadelphia
  • fi 1 dabalataa
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Umuriin hundi · Saalaa hunda · Haaromfame 14-Elb-2026 · NCT00358943

Longitudinal Study of Neurodegenerative Disorders

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
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Umuriin hundi · Saalaa hunda · Haaromfame 09-Gur-2026 · NCT03333200

Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
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2 Months – 60 Years · Saalaa hunda · Haaromfame 13-Ama-2026 · NCT04528355

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
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2 Months – 55 Years · Saalaa hunda · Haaromfame 15-Mud-2025 · NCT01962415

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.