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Qorannoo klinikaalii Dhukkuboota Dhalootaa North Carolina keessatti
Qorannoo 9 Dhukkuboota Dhalootaa f North Carolina keessatti hirmaatuu jiru.
Magaalota North Carolina keessatti
Takkalaa qorannoo (Ingiliffa)
Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network
- Duke University Health System, Durham
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1 Month – 100 Years · Saalaa hunda · Haaromfame 02-Onk-2026 · NCT02450851Inherited Reproductive Disorders
- NIEHS Clinical Research Unit (CRU), Research Triangle Park
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6 Weeks – 120 Years · Saalaa hunda · Haaromfame 28-Ado-2026 · NCT01500447Rett Syndrome Registry
- The University of North Carolina at Chapel Hill, Chapel Hill
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Umuriin 0 hanga 99 · Saalaa hunda · Haaromfame 30-Wax-2026 · NCT05432349Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO)
- Rare Disease Research, LLC, Hillsborough
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Umuriin 4 hanga 18 · Dhiroota · Haaromfame 27-Cam-2026 · NCT07608432Helix Research Network
- Cone Health (Gene Connect), Burlington
- WakeMed (PreciselyYou), Raleigh
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Umuriin 18 fi ol · Saalaa hunda · Haaromfame 23-Bit-2026 · NCT06057181A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study
- Duke University Medical System (Duke Health), Durham
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Umuriin 1 fi ol · Saalaa hunda · Haaromfame 23-Bit-2026 · NCT05130437Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease
- Levine Children's Hospital - Hematology, Charlotte
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Umuriin 12 hanga 35 · Saalaa hunda · Haaromfame 23-Bit-2026 · NCT05477563PKP2-ACM Natural History Study
- Duke University, Durham
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Umuriin 12 fi ol · Saalaa hunda · Haaromfame 27-Gur-2026 · NCT06644742Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia
- Duke University Medical System (Duke Health), Durham
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Umuriin hundi · Saalaa hunda · Haaromfame 22-Ama-2026 · NCT04159103Kanneen ClinicalTrials.gov irraa argaman, daataa 05-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.