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Qorannoo klinikaalii Dhukkuboota Dhalootaa North Carolina keessatti

Qorannoo 9 Dhukkuboota Dhalootaa f North Carolina keessatti hirmaatuu jiru.

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Takkalaa qorannoo (Ingiliffa)

Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network

  • Duke University Health System, Durham
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1 Month – 100 Years · Saalaa hunda · Haaromfame 02-Onk-2026 · NCT02450851

Inherited Reproductive Disorders

  • NIEHS Clinical Research Unit (CRU), Research Triangle Park
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6 Weeks – 120 Years · Saalaa hunda · Haaromfame 28-Ado-2026 · NCT01500447

Rett Syndrome Registry

  • The University of North Carolina at Chapel Hill, Chapel Hill
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Umuriin 0 hanga 99 · Saalaa hunda · Haaromfame 30-Wax-2026 · NCT05432349

Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO)

  • Rare Disease Research, LLC, Hillsborough
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Umuriin 4 hanga 18 · Dhiroota · Haaromfame 27-Cam-2026 · NCT07608432

Helix Research Network

  • Cone Health (Gene Connect), Burlington
  • WakeMed (PreciselyYou), Raleigh
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Umuriin 18 fi ol · Saalaa hunda · Haaromfame 23-Bit-2026 · NCT06057181

A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study

  • Duke University Medical System (Duke Health), Durham
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Umuriin 1 fi ol · Saalaa hunda · Haaromfame 23-Bit-2026 · NCT05130437

Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease

  • Levine Children's Hospital - Hematology, Charlotte
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Umuriin 12 hanga 35 · Saalaa hunda · Haaromfame 23-Bit-2026 · NCT05477563

PKP2-ACM Natural History Study

  • Duke University, Durham
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Umuriin 12 fi ol · Saalaa hunda · Haaromfame 27-Gur-2026 · NCT06644742

Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia

  • Duke University Medical System (Duke Health), Durham
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Umuriin hundi · Saalaa hunda · Haaromfame 22-Ama-2026 · NCT04159103

Kanneen ClinicalTrials.gov irraa argaman, daataa 05-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.